Simone Merlin
Novara, Italy
Last Updated: 09/26/2026
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Found 35 publications
Myeloid Cell Function and Cytokine Profiles in Paediatric Haemophilia A: Insights From FVIII and Emicizumab Prophylaxis.
Journal: Journal of cellular and molecular medicine
Published: December 12, 2025
Balancing Promise and Peril: Hemophilia Gene Therapy Insights.
Journal: IUBMB life
Published: April 09, 2025
Factor VIII promotes angiogenesis and vessel stability regulating extracellular matrix proteins.
Journal: Haematologica
Published: January 22, 2024
GP64-pseudotyped lentiviral vectors target liver endothelial cells and correct hemophilia A mice.
Journal: EMBO molecular medicine
Published: September 06, 2023
Immune tolerance promotion by LSEC-specific lentiviral vector-mediated expression of the transgene regulated by the stabilin-2 promoter.
Journal: Molecular therapy. Nucleic acids
Published: March 29, 2023
Durable and efficient gene silencing in vivo by hit-and-run epigenome editing.
Journal: Nature
Published: March 06, 2023
Therapeutic potential of fetal liver cell transplantation in hemophilia A mice.
Journal: Haematologica
Published: August 31, 2022
Liver gene therapy with intein-mediated F8 trans-splicing corrects mouse haemophilia A.
Journal: EMBO molecular medicine
Published: October 13, 2021
Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device.
Journal: Molecular therapy. Methods & clinical development
Published: June 30, 2021
Dissection of pleiotropic effects of variants in and adjacent to F8 exon 19 and rescue of mRNA splicing and protein function.
Journal: American journal of human genetics
Published: March 16, 2021
Last Updated: 09/26/2026