Stefan Spinty
Liverpool, ENG, United Kingdom
Last Updated: 09/26/2026
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Found 33 publications
Safety and Efficacy of Tamoxifen in Patients with Duchenne muscular dystrophy: open Label Extension of TAMDMD Trial.
Journal: Neuromuscular disorders : NMD
Published: October 15, 2025
Preventing Cardiomyopathy in Duchenne Muscular Dystrophy: Long-Term Follow-Up of Patients in the Randomised, Placebo-Controlled Drug-Trial of Perindopril and Bisoprolol.
Journal: European journal of neurology
Published: November 08, 2024
Safety and efficacy of tamoxifen in non-ambulant patients with Duchenne muscular dystrophy: a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial (TAMDMD Group B).
Journal: Neuromuscular disorders : NMD
Published: September 16, 2024
Multidisciplinary Care for Moebius Syndrome and Related Disorders: Building a Management Protocol.
Journal: Journal of clinical medicine
Published: April 06, 2024
Risdiplam in Spinal Muscular Atrophy: Safety Profile and Use Through The Early Access to Medicine Scheme for the Paediatric Cohort in Great Britain.
Journal: Journal of neuromuscular diseases
Published: January 08, 2024
Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial.
Journal: The Lancet. Neurology
Published: September 25, 2023
Safety and efficacy of tamoxifen in boys with Duchenne muscular dystrophy (TAMDMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial.
Journal: The Lancet. Neurology
Published: March 16, 2023
Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial.
Journal: JAMA neurology
Published: August 29, 2022
Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial.
Journal: JAMA
Published: April 05, 2022
Communicating hydrocephalus and raised intracranial pressure in association with multi-systemic smooth muscle dysfunction syndrome (MSMDS).
Journal: Child's nervous system : ChNS : official journal of the International Society for Pediatric Neurosurgery
Published: March 17, 2022
British Society for Rheumatology guideline on management of paediatric, adolescent and adult patients with idiopathic inflammatory myopathy.
Journal: Rheumatology (Oxford, England)
Published: July 06, 2021
Last Updated: 09/26/2026