Last Updated: 09/26/2026
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Found 5 publications
Base Editing of HBG1 and HBG2 Promoters for Sickle Cell Disease.
Journal: The New England journal of medicine
Published: April 03, 2026
Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease.
Journal: The New England journal of medicine
Published: December 13, 2021
Acute Myeloid Leukemia Case after Gene Therapy for Sickle Cell Disease.
Journal: The New England journal of medicine
Published: December 13, 2021
Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis.
Journal: The New England journal of medicine
Published: July 05, 2018
A randomized, double-blind, placebo-controlled, dose-ranging study using Genz-644470 and sevelamer carbonate in hyperphosphatemic chronic kidney disease patients on hemodialysis.
Journal: International journal of nephrology and renovascular disease
Published: April 22, 2014
Showing 1-5 of 5
Last Updated: 09/26/2026