Svetlana A. Smirnikhina

1, Moskvorechye Str
Moscow, MOW 115522, Russian Federation

Last Updated: 09/26/2026

Save publications for later

Sign Up

Not sure about your diagnosis?

Check Your Symptoms

Found 67 publications

Cellular Models and Functional Assays for Assessing CFTR Function: A Comprehensive Review.

Cellular Models and Functional Assays for Assessing CFTR Function: A Comprehensive Review.

Journal: International journal of molecular sciences

Published: May 06, 2026

Extracellular vesicle-based delivery to airway basal cells for durable gene therapy in cystic fibrosis.

Extracellular vesicle-based delivery to airway basal cells for durable gene therapy in cystic fibrosis.

Journal: Frontiers in bioengineering and biotechnology

Published: April 14, 2026

Oncogenesis as an Adverse Effect of Gene Replacement Therapy in Hematopoietic Stem Cells.

Oncogenesis as an Adverse Effect of Gene Replacement Therapy in Hematopoietic Stem Cells.

Journal: International journal of molecular sciences

Published: April 09, 2026

Clinical and Molecular Characterization of TCIRG1-Related Autosomal Recessive Osteopetrosis with Current Therapeutic Approaches.

Clinical and Molecular Characterization of TCIRG1-Related Autosomal Recessive Osteopetrosis with Current Therapeutic Approaches.

Journal: Biomedicines

Published: March 11, 2026

Genomic Context and Insert Orientation in the Regulation of Transgene Expression in Adenoviral Vectors.

Genomic Context and Insert Orientation in the Regulation of Transgene Expression in Adenoviral Vectors.

Journal: International journal of molecular sciences

Published: February 23, 2026

Optimized ND4 allotopic expression for gene therapy of Leber's hereditary optic neuropathy.

Optimized ND4 allotopic expression for gene therapy of Leber's hereditary optic neuropathy.

Journal: Frontiers in bioengineering and biotechnology

Published: December 11, 2025

Targeting of Human Mitochondrial DNA with Programmable pAgo Nuclease.

Targeting of Human Mitochondrial DNA with Programmable pAgo Nuclease.

Journal: Cells

Published: December 04, 2025

The Promise and Pitfalls of AAV-Mediated Gene Therapy for Duchenne Muscular Dystrophy.

The Promise and Pitfalls of AAV-Mediated Gene Therapy for Duchenne Muscular Dystrophy.

Journal: Current issues in molecular biology

Published: December 01, 2025

Transcriptomic Profile of Directed Differentiation of iPSCs into Hepatocyte-like Cells.

Transcriptomic Profile of Directed Differentiation of iPSCs into Hepatocyte-like Cells.

Journal: International journal of molecular sciences

Published: October 18, 2025

Allogeneic Hematopoietic Stem Cell Transplantation as a Therapeutic Approach for Hereditary Diseases.

Allogeneic Hematopoietic Stem Cell Transplantation as a Therapeutic Approach for Hereditary Diseases.

Journal: Biomedicines

Published: October 13, 2025

Ex Vivo Gene and Cell Therapy in Hematopoietic Stem Cells.

Ex Vivo Gene and Cell Therapy in Hematopoietic Stem Cells.

Journal: International journal of molecular sciences

Published: October 07, 2025

Methodological landscape in the field of integration site identification of retroviruses and retroviral vectors.

Methodological landscape in the field of integration site identification of retroviruses and retroviral vectors.

Journal: Frontiers in bioengineering and biotechnology

Published: September 19, 2025

Showing 1-12 of 67

Last Updated: 09/26/2026