Sydney Steiman
Toronto, ON M5S1A8, Canada
Last Updated: 09/26/2026
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Found 8 publications
Restoring the Balance: CRISPRa-Driven β-Tubulin Compensation as a Strategy for Tubulinopathy Treatment.
Journal: International journal of molecular sciences
Published: June 25, 2026
Bridging the gap: an emerging link between tubulinopathies and ciliopathies.
Journal: NPJ genomic medicine
Published: November 18, 2025
A novel humanized mouse model exhibits neurobehavioral impairments and recapitulates key neuropathological features of infantile Tay-Sachs disease.
Journal: Journal of neuroinflammation
Published: November 11, 2025
Correction: A novel mouse model of Duchenne muscular dystrophy carrying a multi-exonic Dmd deletion exhibits progressive muscular dystrophy and early-onset cardiomyopathy.
Journal: Disease models & mechanisms
Published: April 04, 2025
FoxP1 Represses MEF2A in Striated Muscle.
Journal: Molecular and cellular biology
Published: March 14, 2024
Multi-gene duplication removal in an engineered human cellular MECP2 duplication syndrome model with an IRAK1-MECP2 duplication.
Journal: Molecular therapy. Nucleic acids
Published: December 01, 2023
Mutations in the β-tubulin TUBB impair ciliogenesis and are associated with ciliopathy-like phenotypes.
Journal: Nature communications
Published: June 16, 2023
A novel mouse model of Duchenne muscular dystrophy carrying a multi-exonic Dmd deletion exhibits progressive muscular dystrophy and early-onset cardiomyopathy.
Journal: Disease models & mechanisms
Published: April 24, 2020
Showing 1-8 of 8
Last Updated: 09/26/2026