Talita G. De Carvalho

Porto Alegre, RS, Brazil

Last Updated: 09/26/2026

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Found 13 publications

Gene Therapy of Mucopolysaccharidosis Type I Mice: Repeated Administrations and Safety Assessment of pIDUA/Nanoemulsion Complexes.

Gene Therapy of Mucopolysaccharidosis Type I Mice: Repeated Administrations and Safety Assessment of pIDUA/Nanoemulsion Complexes.

Journal: Current gene therapy
Published: September 18, 2020

Nasal Administration of Cationic Nanoemulsions as Nucleic Acids Delivery Systems Aiming at Mucopolysaccharidosis Type I Gene Therapy.

Nasal Administration of Cationic Nanoemulsions as Nucleic Acids Delivery Systems Aiming at Mucopolysaccharidosis Type I Gene Therapy.

Journal: Pharmaceutical research
Published: May 15, 2018

CRISPR-Cas9-mediated gene editing in human MPS I fibroblasts.

CRISPR-Cas9-mediated gene editing in human MPS I fibroblasts.

Journal: Gene
Published: May 02, 2018

Gene editing of MPS I human fibroblasts by co-delivery of a CRISPR/Cas9 plasmid and a donor oligonucleotide using nanoemulsions as nonviral carriers.

Gene editing of MPS I human fibroblasts by co-delivery of a CRISPR/Cas9 plasmid and a donor oligonucleotide using nanoemulsions as nonviral carriers.

Journal: European journal of pharmaceutics and biopharmaceutics : official journal of Arbeitsgemeinschaft fur Pharmazeutische Verfahrenstechnik e.V
Published: June 01, 2017

A simple protocol for transfecting human mesenchymal stem cells.

A simple protocol for transfecting human mesenchymal stem cells.

Journal: Biotechnology letters
Published: May 28, 2017

Factors influencing transfection efficiency of pIDUA/nanoemulsion complexes in a mucopolysaccharidosis type I murine model.

Factors influencing transfection efficiency of pIDUA/nanoemulsion complexes in a mucopolysaccharidosis type I murine model.

Journal: International journal of nanomedicine
Published: March 30, 2017

Cationic Nanoemulsions as a Gene Delivery System: Proof of Concept in the Mucopolysaccharidosis I Murine Model.

Cationic Nanoemulsions as a Gene Delivery System: Proof of Concept in the Mucopolysaccharidosis I Murine Model.

Journal: Journal of nanoscience and nanotechnology
Published: September 03, 2015

PEGylated cationic nanoemulsions can efficiently bind and transfect pIDUA in a mucopolysaccharidosis type I murine model.

PEGylated cationic nanoemulsions can efficiently bind and transfect pIDUA in a mucopolysaccharidosis type I murine model.

Journal: Journal of controlled release : official journal of the Controlled Release Society
Published: October 24, 2014

Effects of enzyme replacement therapy started late in a murine model of mucopolysaccharidosis type I.

Effects of enzyme replacement therapy started late in a murine model of mucopolysaccharidosis type I.

Journal: PloS one
Published: June 24, 2014

Laronidase-functionalized multiple-wall lipid-core nanocapsules: promising formulation for a more effective treatment of mucopolysaccharidosis type I.

Laronidase-functionalized multiple-wall lipid-core nanocapsules: promising formulation for a more effective treatment of mucopolysaccharidosis type I.

Journal: Pharmaceutical research
Published: May 17, 2014

Increased glutamate receptor and transporter expression in the cerebral cortex and striatum of gcdh-/- mice: possible implications for the neuropathology of glutaric acidemia type I.

Increased glutamate receptor and transporter expression in the cerebral cortex and striatum of gcdh-/- mice: possible implications for the neuropathology of glutaric acidemia type I.

Journal: PloS one
Published: June 28, 2013

Treatment of MPS I mice with microencapsulated cells overexpressing IDUA: effect of the prednisolone administration.

Treatment of MPS I mice with microencapsulated cells overexpressing IDUA: effect of the prednisolone administration.

Journal: Journal of microencapsulation
Published: February 20, 2013
Showing 1-12 of 13

Last Updated: 09/26/2026