Last Updated: 09/26/2026
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Found 181 publications
Accelerated design of antiviral peptides to clamp down on emerging pathogens.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: July 13, 2026
Endothelial injury with capillary leak: A final common pathway in acute AAV toxicity?
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: June 07, 2026
The dose makes the poison: Mechanisms of cytotoxicity of high-dose AAV vectors.
Journal: Molecular therapy. Advances
Published: May 22, 2026
Optimization of Alpha-1 Antitrypsin Expression from Adeno-Associated Virus Vectors.
Journal: Human gene therapy
Published: May 20, 2026
Letter to the Editor. Intrathalamic gene delivery.
Journal: Journal of neurosurgery
Published: May 01, 2026
Immune Toxicities in AAV Gene Therapy: Overview for Clinicians.
Journal: International journal of molecular sciences
Published: February 23, 2026
AAV9 Gene Therapy in Type II GM1 Gangliosidosis - A Phase 1-2 Trial.
Journal: The New England journal of medicine
Published: February 10, 2026
Maximizing Access to Cell and Gene Therapy for Patients with Rare Diseases.
Journal: Human gene therapy
Published: February 05, 2026
Advances in Precision Editing Therapies for Alpha-1 Antitrypsin Deficiency.
Journal: Human gene therapy
Published: January 27, 2026
Response to the FDA's proposed pathway for individualized genetic therapies.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: December 10, 2025
Overcoming barriers to commercially pre-viable gene and cell therapies for rare and ultra-rare diseases.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: August 12, 2025
Last Updated: 09/26/2026