Theodora Markati
Oxford, ENG, United Kingdom
Last Updated: 09/26/2026
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Found 10 publications
The use of digital outcome measures in clinical trials in rare neurological diseases: a systematic literature review.
Journal: Orphanet journal of rare diseases
Published: April 13, 2023
Early clinical and pre-clinical therapy development in Nemaline myopathy.
Journal: Expert opinion on therapeutic targets
Published: December 16, 2022
A systematic review of adeno-associated virus gene therapies in neurology: the need for consistent safety monitoring of a promising treatment.
Journal: Journal of neurology, neurosurgery, and psychiatry
Published: April 18, 2022
Risdiplam: an investigational survival motor neuron 2 (SMN2) splicing modifier for spinal muscular atrophy (SMA).
Journal: Expert opinion on investigational drugs
Published: March 22, 2022
Lessons Learned from Discontinued Clinical Developments in Duchenne Muscular Dystrophy.
Journal: Frontiers in pharmacology
Published: July 03, 2021
Therapies in preclinical and clinical development for Angelman syndrome.
Journal: Expert opinion on investigational drugs
Published: June 11, 2021
Emerging therapies for Duchenne muscular dystrophy.
Journal: The Lancet. Neurology
Published: June 07, 2021
Pre-emptive opioid sedation during therapeutic hypothermia.
Journal: Archives of disease in childhood. Fetal and neonatal edition
Published: March 27, 2019
Therapeutic hypothermia for mild neonatal encephalopathy: a systematic review and meta-analysis.
Journal: Archives of disease in childhood. Fetal and neonatal edition
Published: June 16, 2018
Showing 1-10 of 10
Last Updated: 09/26/2026