Last Updated: 09/26/2026
Save publications for later
Sign Up
Not sure about your diagnosis?
Check Your Symptoms
Found 72 publications
Clinical outcomes of lentiviral vector gene therapy for sickle cell disease.
Journal: Blood advances
Published: February 02, 2026
Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1.
Journal: Obstetrical & gynecological survey
Published: December 30, 2025
Upper and Lower Respiratory Tract Compartmentalization in Pediatric Stem Cell Transplantation.
Journal: American journal of respiratory cell and molecular biology
Published: December 11, 2025
Upper and Lower Respiratory Tract Compartmentalization in Pediatric Stem Cell Transplantation.
Journal: medRxiv : the preprint server for health sciences
Published: November 24, 2025
Newborn screening reduces survival disparities in SCID after stem cell transplant: A PIDTC report.
Journal: Journal of human immunity
Published: October 27, 2025
Long-Term Safety and Efficacy of Gene Therapy for Adenosine Deaminase Deficiency.
Journal: The New England journal of medicine
Published: October 15, 2025
Hematopoietic cell transplantation for Wiskott-Aldrich syndrome: a PIDTC report.
Journal: Blood advances
Published: July 02, 2025
Hematopoietic Cell Transplantation for Wiskott-Aldrich syndrome: A PIDTC Report.
Journal: Blood advances
Published: July 02, 2025
Integrating pulmonary and systemic transcriptomes to characterize lung injury after pediatric hematopoietic stem cell transplant.
Journal: JCI insight
Published: May 05, 2025
Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1.
Journal: The New England journal of medicine
Published: April 30, 2025
Last Updated: 09/26/2026