Tippi C. Mackenzie

Tippi C. Mackenzie

General Surgery

1855 Fourth St.
Second Floor, Room A-2432
San Francisco, CA 94158

Last Updated: 09/26/2026

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Found 85 publications

Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells.

Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells.

Journal: bioRxiv : the preprint server for biology

Published: April 27, 2026

Evidence for Maternal Autoantibodies in the Pathogenesis of Preterm Birth.

Evidence for Maternal Autoantibodies in the Pathogenesis of Preterm Birth.

Journal: medRxiv : the preprint server for health sciences

Published: January 22, 2026

In utero hematopoietic cell transplantation in fetuses with α-thalassemia major: a phase 1 clinical trial.

In utero hematopoietic cell transplantation in fetuses with α-thalassemia major: a phase 1 clinical trial.

Journal: Blood advances

Published: January 08, 2026

Attitudes Toward Prenatal Interventions in the Fanconi Anemia Community.

Attitudes Toward Prenatal Interventions in the Fanconi Anemia Community.

Journal: Prenatal diagnosis

Published: September 08, 2025

Integrated single-nuclei and spatial transcriptomic profiling of human sacrococcygeal teratomas reveals heterogeneity in cellular composition and X-chromosome inactivation.

Integrated single-nuclei and spatial transcriptomic profiling of human sacrococcygeal teratomas reveals heterogeneity in cellular composition and X-chromosome inactivation.

Journal: bioRxiv : the preprint server for biology

Published: August 08, 2025

Single nuclei and spatial profiling of sacrococcygeal teratomas reveals cellular composition and X inactivation heterogeneity.

Single nuclei and spatial profiling of sacrococcygeal teratomas reveals cellular composition and X inactivation heterogeneity.

Journal: NPJ precision oncology

Published: August 04, 2025

In utero genetic therapy: Treatment of early onset neurological disorders before they start.

In utero genetic therapy: Treatment of early onset neurological disorders before they start.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: June 09, 2025

In utero lipid nanoparticle delivery achieves robust editing in hematopoietic stem cells.

In utero lipid nanoparticle delivery achieves robust editing in hematopoietic stem cells.

Journal: bioRxiv : the preprint server for biology

Published: June 04, 2025

Intra-amniotic antisense oligonucleotide treatment improves phenotypes in preclinical models of spinal muscular atrophy.

Intra-amniotic antisense oligonucleotide treatment improves phenotypes in preclinical models of spinal muscular atrophy.

Journal: Science translational medicine

Published: May 14, 2025

Lentiviral vectors for hematopoietic stem cell gene therapy restore α-globin expression in α-thalassemia red blood cells.

Lentiviral vectors for hematopoietic stem cell gene therapy restore α-globin expression in α-thalassemia red blood cells.

Journal: Cell reports. Medicine

Published: March 24, 2025

Prenatal Delivery of Enzyme Replacement Therapy to Fetuses Affected by Early-Onset Lysosomal Storage Diseases.

Prenatal Delivery of Enzyme Replacement Therapy to Fetuses Affected by Early-Onset Lysosomal Storage Diseases.

Journal: American journal of medical genetics. Part C, Seminars in medical genetics

Published: December 05, 2024

GFP-on mouse model for interrogation of in vivo gene editing.

GFP-on mouse model for interrogation of in vivo gene editing.

Journal: Nature communications

Published: September 26, 2024

Showing 1-12 of 85

Last Updated: 09/26/2026