Tiziana Plati
Milan, 20132, Italy
Last Updated: 09/26/2026
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Found 9 publications
Identification of hepatocyte-primed cholangiocytes in the homeostatic liver by in vivo lentiviral gene transfer to mice and non-human primates.
Journal: Cell reports
Published: May 16, 2023
Liver-directed lentiviral gene therapy corrects hemophilia A mice and achieves normal-range factor VIII activity in non-human primates.
Journal: Nature communications
Published: August 30, 2021
Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1.
Journal: Science translational medicine
Published: March 01, 2017
miRNA-126 Orchestrates an Oncogenic Program in B Cell Precursor Acute Lymphoblastic Leukemia.
Journal: Cancer cell
Published: May 29, 2015
MicroRNA-223 dose levels fine tune proliferation and differentiation in human cord blood progenitors and acute myeloid leukemia.
Journal: Experimental hematology
Published: May 03, 2015
Shedding of clinical-grade lentiviral vectors is not detected in a gene therapy setting.
Journal: Gene therapy
Published: October 03, 2014
Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy.
Journal: Science (New York, N.Y.)
Published: July 13, 2013
Brain conditioning is instrumental for successful microglia reconstitution following hematopoietic stem cell transplantation.
Journal: Proceedings of the National Academy of Sciences of the United States of America
Published: August 28, 2012
Showing 1-9 of 9
Last Updated: 09/26/2026