Valentina Vavassori
Milan, 20132, Italy
Last Updated: 09/26/2026
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Found 13 publications
Exonic knockout and knockin gene editing in hematopoietic stem and progenitor cells rescues RAG1 immunodeficiency.
Journal: Science translational medicine
Published: February 07, 2024
TIM-3, LAG-3, or 2B4 gene disruptions increase the anti-tumor response of engineered T cells.
Journal: Frontiers in immunology
Published: October 10, 2023
Scalable GMP-compliant gene correction of CD4+ T cells with IDLV template functionally validated in vitro and in vivo.
Journal: Molecular therapy. Methods & clinical development
Published: May 25, 2023
Unbiased assessment of genome integrity and purging of adverse outcomes at the target locus upon editing of CD4+ T-cells for the treatment of Hyper IgM1.
Journal: The EMBO journal
Published: April 04, 2023
Lipid nanoparticles allow efficient and harmless ex vivo gene editing of human hematopoietic cells.
Journal: Blood
Published: December 05, 2022
Mesenchymal stromal cells improve the transplantation outcome of CRISPR-Cas9 gene-edited human HSPCs.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: September 12, 2022
Mesenchymal stromal cells improve the transplantation outcome of CRISPR-Cas9 gene-edited human HSPCs.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: February 25, 2022
Mobilization-based chemotherapy-free engraftment of gene-edited human hematopoietic stem cells.
Journal: Cell
Published: December 16, 2021
Gene Editing of Hematopoietic Stem Cells: Hopes and Hurdles Toward Clinical Translation.
Journal: Frontiers in genome editing
Published: October 16, 2020
Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper-IgM syndrome.
Journal: EMBO molecular medicine
Published: October 06, 2020
Efficient gene editing of human long-term hematopoietic stem cells validated by clonal tracking.
Journal: Nature biotechnology
Published: December 06, 2019
Last Updated: 09/26/2026