Last Updated: 09/26/2026
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Found 8 publications
Fair, just and compassionate: A pilot for making allocation decisions for patients requesting experimental drugs outside of clinical trials.
Journal: Journal of medical ethics
Published: March 15, 2018
Efficacy and safety of deflazacort vs prednisone and placebo for Duchenne muscular dystrophy.
Journal: Neurology
Published: March 10, 2016
Clinical Follow-Up for Duchenne Muscular Dystrophy Newborn Screening: A Proposal.
Journal: Muscle & nerve
Published: February 01, 2016
Perspectives on best practices for gene therapy programs.
Journal: Human gene therapy
Published: February 06, 2015
Can outcomes in Duchenne muscular dystrophy be improved by public reporting of data?
Journal: Neurology
Published: November 13, 2013
Corticosteroids in Duchenne muscular dystrophy: major variations in practice.
Journal: Muscle & nerve
Published: March 01, 2013
Cost of illness for neuromuscular diseases in the United States.
Journal: Muscle & nerve
Published: February 27, 2013
Can outcomes in Duchenne muscular dystrophy be improved by public reporting of data?
Journal: Neurology
Published: February 06, 2013
Showing 1-8 of 8
Last Updated: 09/26/2026