Valerie Ferreira

Amsterdam, NH, Netherlands

Last Updated: 09/26/2026

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Found 13 publications

miRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3.

miRNA-Mediated Knockdown of ATXN3 Alleviates Molecular Disease Hallmarks in a Mouse Model for Spinocerebellar Ataxia Type 3.

Journal: Nucleic acid therapeutics

Published: December 08, 2021

Cell-Based Tracers as Trojan Horses for Image-Guided Surgery.

Cell-Based Tracers as Trojan Horses for Image-Guided Surgery.

Journal: International journal of molecular sciences

Published: December 17, 2020

Clinical Considerations for Capsid Choice in the Development of Liver-Targeted AAV-Based Gene Transfer.

Clinical Considerations for Capsid Choice in the Development of Liver-Targeted AAV-Based Gene Transfer.

Journal: Molecular therapy. Methods & clinical development

Published: October 30, 2019

Enhanced Factor IX Activity following Administration of AAV5-R338L "Padua" Factor IX versus AAV5 WT Human Factor IX in NHPs.

Enhanced Factor IX Activity following Administration of AAV5-R338L "Padua" Factor IX versus AAV5 WT Human Factor IX in NHPs.

Journal: Molecular therapy. Methods & clinical development

Published: May 17, 2019

Immunoadsorption enables successful rAAV5-mediated repeated hepatic gene delivery in nonhuman primates.

Immunoadsorption enables successful rAAV5-mediated repeated hepatic gene delivery in nonhuman primates.

Journal: Blood advances

Published: April 29, 2019

Therapeutic hFIX Activity Achieved after Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs.

Therapeutic hFIX Activity Achieved after Single AAV5-hFIX Treatment in Hemophilia B Patients and NHPs with Pre-existing Anti-AAV5 NABs.

Journal: Molecular therapy. Methods & clinical development

Published: April 08, 2019

Successful Repeated Hepatic Gene Delivery in Mice and Non-human Primates Achieved by Sequential Administration of AAV5ch and AAV1.

Successful Repeated Hepatic Gene Delivery in Mice and Non-human Primates Achieved by Sequential Administration of AAV5ch and AAV1.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: October 12, 2016

Recombinant AAV Integration Is Not Associated With Hepatic Genotoxicity in Nonhuman Primates and Patients.

Recombinant AAV Integration Is Not Associated With Hepatic Genotoxicity in Nonhuman Primates and Patients.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: December 18, 2015

Immune responses to intramuscular administration of alipogene tiparvovec (AAV1-LPL(S447X)) in a phase II clinical trial of lipoprotein lipase deficiency gene therapy.

Immune responses to intramuscular administration of alipogene tiparvovec (AAV1-LPL(S447X)) in a phase II clinical trial of lipoprotein lipase deficiency gene therapy.

Journal: Human gene therapy

Published: December 05, 2013

Immune Responses to AAV-Vectors, the Glybera Example from Bench to Bedside.

Immune Responses to AAV-Vectors, the Glybera Example from Bench to Bedside.

Journal: Frontiers in immunology

Published: September 09, 2013

Mir-142-3p target sequences reduce transgene-directed immunogenicity following intramuscular adeno-associated virus 1 vector-mediated gene delivery.

Mir-142-3p target sequences reduce transgene-directed immunogenicity following intramuscular adeno-associated virus 1 vector-mediated gene delivery.

Journal: The journal of gene medicine

Published: November 29, 2012

Murine CD4⁺CD25⁻ cells activated in vitro with PMA/ionomycin and anti-CD3 acquire regulatory function and ameliorate experimental colitis in vivo.

Murine CD4⁺CD25⁻ cells activated in vitro with PMA/ionomycin and anti-CD3 acquire regulatory function and ameliorate experimental colitis in vivo.

Journal: BMC gastroenterology

Published: July 16, 2012

Showing 1-12 of 13

Last Updated: 09/26/2026