Last Updated: 09/26/2026
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Found 18 publications
Clinically meaningful improvements in patient-reported outcomes in mitapivat-treated patients with pyruvate kinase deficiency.
Journal: American journal of hematology
Published: September 29, 2023
Defective Induction of IL-27-Mediated Immunoregulation by Myeloid DCs in Multiple Sclerosis.
Journal: International journal of molecular sciences
Published: February 09, 2023
Mitapivat versus Placebo for Pyruvate Kinase Deficiency. Reply.
Journal: The New England journal of medicine
Published: June 29, 2022
Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial.
Journal: The Lancet. Haematology
Published: April 22, 2022
Mitapivat versus Placebo for Pyruvate Kinase Deficiency.
Journal: The New England journal of medicine
Published: April 13, 2022
Chronic lesion activity and disability progression in secondary progressive multiple sclerosis.
Journal: BMJ neurology open
Published: November 02, 2021
microRNA-92a promotes CNS autoimmunity by modulating the regulatory and inflammatory T cell balance.
microRNA-92a promotes CNS autoimmunity by modulating the regulatory and inflammatory T cell balance.
Journal: The Journal of clinical investigation
Published: October 12, 2021
Delayed-Release Dimethyl Fumarate Safety and Efficacy in Pediatric Patients With Relapsing-Remitting Multiple Sclerosis.
Journal: Frontiers in neurology
Published: September 14, 2020
Patterning Chronic Active Demyelination in Slowly Expanding/Evolving White Matter MS Lesions.
Journal: AJNR. American journal of neuroradiology
Published: February 26, 2020
Smad7 Controls Immunoregulatory PDL2/1-PD1 Signaling in Intestinal Inflammation and Autoimmunity.
Journal: Cell reports
Published: October 23, 2018
Monomethyl fumarate treatment impairs maturation of human myeloid dendritic cells and their ability to activate T cells.
Journal: Multiple sclerosis (Houndmills, Basingstoke, England)
Published: November 07, 2017
Last Updated: 09/26/2026