Last Updated: 09/26/2026
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Found 5 publications
Investigating Immune Responses to the scAAV9-HEXM Gene Therapy Treatment in Tay-Sachs Disease and Sandhoff Disease Mouse Models.
Journal: International journal of molecular sciences
Published: May 17, 2021
The effects of huntingtin-lowering: what do we know so far?
Journal: Degenerative neurological and neuromuscular disease
Published: March 19, 2019
Onset Time and Durability of Huntingtin Suppression in Rhesus Putamen After Direct Infusion of Antihuntingtin siRNA.
Journal: Molecular therapy. Nucleic acids
Published: October 07, 2014
Six-month partial suppression of Huntingtin is well tolerated in the adult rhesus striatum.
Journal: Brain : a journal of neurology
Published: January 19, 2012
Showing 1-5 of 5
Last Updated: 09/26/2026