William Lostal
Evry, 91000, France
Last Updated: 09/26/2026
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Found 13 publications
Assessment of Therapeutic Potential of a Dual AAV Approach for Duchenne Muscular Dystrophy.
Journal: International journal of molecular sciences
Published: June 04, 2023
Co-Administration of Simvastatin Does Not Potentiate the Benefit of Gene Therapy in the mdx Mouse Model for Duchenne Muscular Dystrophy.
Journal: International journal of molecular sciences
Published: December 08, 2021
Titin M-line insertion sequence 7 is required for proper cardiac function in mice.
Journal: Journal of cell science
Published: March 25, 2021
Minimal Consequences of CMAH and DBA/2 Backgrounds on a FKRP Deficient Model.
Journal: Journal of neuromuscular diseases
Published: September 14, 2020
Single SERCA2a Therapy Ameliorated Dilated Cardiomyopathy for 18 Months in a Mouse Model of Duchenne Muscular Dystrophy.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: July 23, 2019
Titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy type 2A.
Journal: Science translational medicine
Published: January 30, 2019
In Vivo Monitoring of Calpain Activity by Forster Resonance Energy Transfer.
Journal: Methods in molecular biology (Clifton, N.J.)
Published: January 09, 2019
233rd ENMC International Workshop:: Clinical Trial Readiness for Calpainopathies, Naarden, The Netherlands, 15-17 September 2017.
Journal: Neuromuscular disorders : NMD
Published: January 19, 2018
Circulating miRNAs are generic and versatile therapeutic monitoring biomarkers in muscular dystrophies.
Journal: Scientific reports
Published: February 09, 2016
A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence.
Journal: Molecular therapy. Methods & clinical development
Published: June 26, 2014
Full-length dystrophin reconstitution with adeno-associated viral vectors.
Journal: Human gene therapy
Published: March 04, 2014
Last Updated: 09/26/2026