Wouter Beumer

Rotterdam, ZH, Netherlands

Last Updated: 09/26/2026

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Found 20 publications

Cholesterol Conjugation Strategies to Enhance In Vivo Antisense Oligonucleotide-Mediated Exon Skipping in the Mouse Retina.

Cholesterol Conjugation Strategies to Enhance In Vivo Antisense Oligonucleotide-Mediated Exon Skipping in the Mouse Retina.

Journal: Journal of ocular pharmacology and therapeutics : the official journal of the Association for Ocular Pharmacology and Therapeutics
Published: July 20, 2026

The Power of Peers: How Sexual Norms Shape Adolescents' Emotional Responses to Sexual Experiences.

The Power of Peers: How Sexual Norms Shape Adolescents' Emotional Responses to Sexual Experiences.

Journal: Journal of sex research
Published: April 27, 2026

ADAR RNA editing for cardiovascular disease: Targeting B4GALT1 to modulate lipid metabolism through reduced galactosyltransferase activity.

ADAR RNA editing for cardiovascular disease: Targeting B4GALT1 to modulate lipid metabolism through reduced galactosyltransferase activity.

Journal: Molecular therapy. Nucleic acids
Published: October 30, 2025

Antisense oligonucleotide therapy corrects splicing in the common Stargardt disease type 1-causing variant ABCA4 c.5461-10T>C.

Antisense oligonucleotide therapy corrects splicing in the common Stargardt disease type 1-causing variant ABCA4 c.5461-10T>C.

Journal: Molecular therapy. Nucleic acids
Published: October 11, 2022

A pathogenic proteolysis-resistant huntingtin isoform induced by an antisense oligonucleotide maintains huntingtin function.

A pathogenic proteolysis-resistant huntingtin isoform induced by an antisense oligonucleotide maintains huntingtin function.

Journal: JCI insight
Published: August 12, 2021

Antisense oligonucleotide-based treatment of retinitis pigmentosa caused by USH2A exon 13 mutations.

Antisense oligonucleotide-based treatment of retinitis pigmentosa caused by USH2A exon 13 mutations.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: February 12, 2021

Animal models for cystic fibrosis: a systematic search and mapping review of the literature. Part 2: nongenetic models.

Animal models for cystic fibrosis: a systematic search and mapping review of the literature. Part 2: nongenetic models.

Journal: Laboratory animals
Published: February 09, 2021

Improving Translation by Identifying Evidence for More Human-Relevant Preclinical Strategies.

Improving Translation by Identifying Evidence for More Human-Relevant Preclinical Strategies.

Journal: Animals : an open access journal from MDPI
Published: May 15, 2020

Animal models for cystic fibrosis: A systematic search and mapping review of the literature - Part 1: genetic models.

Animal models for cystic fibrosis: A systematic search and mapping review of the literature - Part 1: genetic models.

Journal: Laboratory animals
Published: August 15, 2019

The Cystic Fibrosis-Like Airway Surface Layer Is not a Significant Barrier for Delivery of Eluforsen to Airway Epithelial Cells.

The Cystic Fibrosis-Like Airway Surface Layer Is not a Significant Barrier for Delivery of Eluforsen to Airway Epithelial Cells.

Journal: Journal of aerosol medicine and pulmonary drug delivery
Published: May 24, 2019

Evaluation of eluforsen, a novel RNA oligonucleotide for restoration of CFTR function in in vitro and murine models of p.Phe508del cystic fibrosis.

Evaluation of eluforsen, a novel RNA oligonucleotide for restoration of CFTR function in in vitro and murine models of p.Phe508del cystic fibrosis.

Journal: PloS one
Published: January 09, 2019

Splice-Modulating Oligonucleotide QR-110 Restores CEP290 mRNA and Function in Human c.2991+1655A>G LCA10 Models.

Splice-Modulating Oligonucleotide QR-110 Restores CEP290 mRNA and Function in Human c.2991+1655A>G LCA10 Models.

Journal: Molecular therapy. Nucleic acids
Published: February 23, 2018
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Last Updated: 09/26/2026