Xiaoyan Dong
Beijing, China
Last Updated: 09/26/2026
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Found 23 publications
AAV9-mediated GAA gene therapy following enzyme replacement therapy discontinuation in children with infantile-onset Pompe disease.
Journal: EClinicalMedicine
Published: May 13, 2026
Protective role of HOXB5-orchestrated mitochondrial homeostasis and mitophagy in cardiomyocytes after ischemia-reperfusion via transcriptionally activating Sirt5.
Journal: Cardiovascular drugs and therapy
Published: September 19, 2025
AAV9-Mediated Gene Therapy for Infantile-Onset Pompe's Disease.
Journal: The New England journal of medicine
Published: June 25, 2025
Evaluation of efficacy and safety of AAV8-ΔC4ATP7B gene therapy in a mutant mouse model of Wilson's disease.
Journal: Molecular therapy. Methods & clinical development
Published: September 16, 2024
Preclinical evaluation of AAV9-coSMN1 gene therapy for spinal muscular atrophy: efficacy and safety in mouse models and non-human primates.
Journal: Molecular medicine (Cambridge, Mass.)
Published: September 08, 2024
Using an In Vivo Mouse Model to Determine the Exclusion Criteria of Preexisting Anti-AAV9 Neutralizing Antibody Titer of Pompe Disease Patients in Clinical Trials.
Journal: Viruses
Published: December 07, 2023
Treatment of SMA type 1 infants using a single-dose AAV9-mediated gene therapy via intrathecal injection of GC101: An open-label, single-arm study.
Journal: Chinese medical journal
Published: October 09, 2023
Intra-Operative Definition of Glioma Infiltrative Margins by Visualizing Immunosuppressive Tumor-Associated Macrophages.
Journal: Advanced science (Weinheim, Baden-Wurttemberg, Germany)
Published: June 19, 2023
AAV-mediated hepatic LPL expression ameliorates severe hypertriglyceridemia and acute pancreatitis in Gpihbp1 deficient mice and rats.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: February 20, 2023
Correction of Familial LCAT Deficiency by AAV-hLCAT Prevents Renal Injury and Atherosclerosis in Hamsters-Brief Report.
Journal: Arteriosclerosis, thrombosis, and vascular biology
Published: May 13, 2021
scAAV2-Mediated C3 Transferase Gene Therapy in a Rat Model with Retinal Ischemia/Reperfusion Injuries.
Journal: Molecular therapy. Methods & clinical development
Published: April 12, 2020
AAV-Mediated ApoC2 Gene Therapy: Reversal of Severe Hypertriglyceridemia and Rescue of Neonatal Death in ApoC2-Deficient Hamsters.
Journal: Molecular therapy. Methods & clinical development
Published: March 20, 2020
Last Updated: 09/26/2026