Last Updated: 09/26/2026
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Found 19 publications
DDX3X overexpression in mice can cause rapid tissue-specific toxicity and mortality.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: February 16, 2026
Progress and challenges in intrathecal gene therapy for neurological disorders.
Journal: EBioMedicine
Published: November 05, 2025
Lumbar Intrathecal Injection of Gene Therapy Vectors for Central Nervous System Targeting in Mice and Rats.
Journal: Journal of visualized experiments : JoVE
Published: June 02, 2025
Direct Vagus Nerve Injection Protocol For Rats.
Journal: Journal of visualized experiments : JoVE
Published: March 31, 2025
Riboflavin transporter deficiency: AAV9-SLC52A2 gene therapy as a new therapeutic strategy.
Journal: Frontiers in cellular neuroscience
Published: November 06, 2024
Focused ultrasound widely broadens AAV-delivered Cas9 distribution and activity.
Journal: Gene therapy
Published: June 18, 2024
Well-defined nanostructures of high entropy alloys for electrocatalysis.
Journal: Exploration (Beijing, China)
Published: December 24, 2023
Tumor Diagnosis and Treatment Based on Stimuli-Responsive Aggregation of Gold Nanoparticles.
Journal: Exploration (Beijing, China)
Published: December 11, 2023
AAV gene therapy for hereditary spastic paraplegia type 50: a phase 1 trial in a single patient.
Journal: Nature medicine
Published: August 02, 2023
Last Updated: 09/26/2026