Last Updated: 09/26/2026
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Found 4 publications
Waning efficacy in a long-term AAV-mediated gene therapy study in the murine model of Krabbe disease.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: November 04, 2020
AAV-Mediated GALC Gene Therapy Rescues Alpha-Synucleinopathy in the Spinal Cord of a Leukodystrophic Lysosomal Storage Disease Mouse Model.
Journal: Frontiers in cellular neuroscience
Published: October 20, 2020
α-Synuclein interacts directly but reversibly with psychosine: implications for α-synucleinopathies.
α-Synuclein interacts directly but reversibly with psychosine: implications for α-synucleinopathies.
Journal: Scientific reports
Published: May 02, 2018
Long-Term Improvement of Neurological Signs and Metabolic Dysfunction in a Mouse Model of Krabbe's Disease after Global Gene Therapy.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: August 15, 2017
Showing 1-4 of 4
Last Updated: 09/26/2026