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Last Updated: 10/31/2025
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Found 137 publications
The SGLT2 Inhibitor Dapagliflozin Disrupts the Cell Cycle at High Concentrations Without Altering Glycosphingolipid (De Novo)Biosynthesis.
Journal: International journal of molecular sciences
Published: August 20, 2025
Increased Lyso-Gb1 Levels in an Obese Splenectomized Gaucher Disease Type 1 Patient Treated with Eliglustat: Unacknowledged Poor Compliance or Underlying Factors.
Journal: Metabolites
Published: May 22, 2025
Pharmacogenomics and rare diseases: optimizing drug development and personalized therapeutics.
Journal: Pharmacogenomics
Published: April 07, 2025
In Vivo Accumulation of Regulatory T Cells Using Eliglustat-Loaded Cryogels.
Journal: Advanced healthcare materials
Published: March 22, 2025
Eliglustat substrate reduction therapy in children with Gaucher disease type 1.
Journal: Frontiers in pediatrics
Published: December 10, 2024
Model-informed repurposing of eliglustat for treatment and prophylaxis of Shiga toxin-producing Escherichia coli hemolytic-uremic syndrome (STEC-HUS) in children.
Journal: Pediatric nephrology (Berlin, Germany)
Published: December 03, 2024
Eliglustat and cardiac comorbidities in Gaucher disease: a pharmacogenomic approach to safety and efficacy.
Journal: Frontiers in medicine
Published: November 26, 2024
Challenges in Gaucher disease: Perspectives from an expert panel.
Journal: Molecular genetics and metabolism
Published: September 28, 2024
UPLC-MS/MS Method for Givinostat in Rat Plasma: Development, Validation, in vivo Pharmacokinetics Study and in vitro Metabolic Stability Research.
Journal: Drug design, development and therapy
Published: September 21, 2024
Inhibiting UGCG prevents PRV infection by decreasing lysosome-associated autophage.
Journal: International journal of biological macromolecules
Published: September 05, 2024
Building Confidence in Physiologically Based Pharmacokinetic Modeling of CYP3A Induction Mediated by Rifampin: An Industry Perspective.
Journal: Clinical pharmacology and therapeutics
Published: June 25, 2024
Presentation of ichthyosis after substrate reduction therapy in Gaucher type 1.
Journal: American journal of medical genetics. Part A
Published: June 18, 2024
Last Updated: 10/31/2025