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Last Updated: 10/31/2025
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Found 21 publications
Patient Perceptions of and Experiences with Risk Evaluation and Mitigation Strategies.
Journal: Clinical pharmacology and therapeutics
Published: July 07, 2025
First successful outcomes of pegvaliase (PALYNZIQ) in children.
Journal: BMC medical genomics
Published: November 13, 2023
Nutrition management of PKU with pegvaliase therapy: update of the web-based PKU nutrition management guideline recommendations.
Journal: Orphanet journal of rare diseases
Published: March 06, 2023
Real-world treatment, dosing, and discontinuation patterns among patients treated with pegvaliase for phenylketonuria: Evidence from dispensing data.
Journal: Molecular genetics and metabolism reports
Published: September 15, 2022
Charles Scriver: Epitome of the physician scientist.
Journal: Molecular genetics and metabolism
Published: September 10, 2022
Present and future of lipid nanoparticle-mRNA technology in phenylketonuria disease treatment.
Journal: International review of cell and molecular biology
Published: September 05, 2022
Genetic etiology and clinical challenges of phenylketonuria.
Journal: Human genomics
Published: March 21, 2022
Preliminary Investigation of Microbiome and Dietary Differences in Patients with Phenylketonuria on Enzyme Substitution Therapy Compared to Traditional Therapies.
Journal: Journal of the Academy of Nutrition and Dietetics
Published: May 12, 2021
Achieving efficacy in subjects with sustained pegvaliase-neutralizing antibody responses.
Journal: Molecular genetics and metabolism
Published: April 16, 2021
Palynziq clinic: One year and 43 patients later.
Journal: Molecular genetics and metabolism
Published: March 03, 2021
Last Updated: 10/31/2025