Eteplirsen
Last Updated: 04/28/2026
Save publications for later
Sign Up
Not sure about your diagnosis?
Check Your Symptoms
Found 178 publications
Advancements from the EVOLVE study for assessing real-world experience with eteplirsen, golodirsen and casimersen for the treatment of DMD.
Journal: Journal of comparative effectiveness research
Published: April 10, 2026
Treatment advances for Duchenne muscular dystrophy.
Journal: Current opinion in pediatrics
Published: April 01, 2026
Small RNA or oligonucleotide drugs and challenges in evaluating drug-drug interactions.
Journal: Frontiers in pharmacology
Published: October 07, 2025
The Utilization, Reimbursement, and Cost of Targeted Therapies for Duchenne Muscular Dystrophy (DMD) in US Medicaid Programs: A Descriptive Trend Analysis from 2017 to 2022.
Journal: Pharmaceutical medicine
Published: September 09, 2025
Association between exon-skipping therapy with eteplirsen and cardiac outcomes in Duchenne muscular dystrophy.
Journal: Journal of neuromuscular diseases
Published: August 20, 2025
In Vivo Evaluation of Single- and Multi-Exon-Skipping in mdx52 Mice.
Journal: Methods in molecular biology (Clifton, N.J.)
Published: July 28, 2025
In Vivo Evaluation of Multiple Exon Skipping with Peptide-PMOs in Cardiac and Skeletal Muscles in Dystrophic Dogs.
Journal: Methods in molecular biology (Clifton, N.J.)
Published: July 28, 2025
Evolution and Breakthroughs in Exon Skipping and Splice Modulation: From Inception to Clinical Success.
Journal: Methods in molecular biology (Clifton, N.J.)
Published: July 28, 2025
Systemic Injection of Peptide-PMOs into Humanized DMD Mice and Detection by RT-PCR and ELISA.
Journal: Methods in molecular biology (Clifton, N.J.)
Published: July 28, 2025
Tips to Design Effective Splice-Switching Antisense Oligonucleotides for Exon Skipping and Exon Inclusion.
Journal: Methods in molecular biology (Clifton, N.J.)
Published: July 28, 2025
Quantitative Evaluation of Exon Skipping in Immortalized Muscle Cells in Vitro.
Journal: Methods in molecular biology (Clifton, N.J.)
Published: July 28, 2025
Creation of DMD Muscle Cell Model Using CRISPR-Cas9 Genome Editing to Test the Efficacy of Antisense-Mediated Exon Skipping.
Journal: Methods in molecular biology (Clifton, N.J.)
Published: July 28, 2025
Last Updated: 04/28/2026