Laronidase
Last Updated: 04/28/2026
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1 clinical trial found
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
Who is this study for: Pregnant women age 18 to 50 carrying fetuses between 18 to 34 weeks gestation diagnosed with lysosomal storage disorders
Enrollment Status: Recruiting
Publish Date: March 17, 2026
Intervention Type: Drug
Study Drug: Aldurazyme (laronidase)
Study Phase: Phase 1
Summary: For detailed information, please view our study website: https://pearltrial.ucsf.edu/ The investigators aims to determine the the maternal and fetal safety and feasibility of in utero fetal enzyme replacement therapy in fetuses with Lysosomal Storage Diseases.
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Last Updated: 04/28/2026