Filters

Term Search
You can select from the dropdown list OR enter your own terms to refine the search.

Last Updated: 10/31/2025

Save publications for later
Sign Up
Not sure about your diagnosis?
Check Your Symptoms
Found 59 publications

Ten-Year Follow-Up of Taliglucerase Alfa in Type 1 Gaucher Disease: Real-World Evidence from Albania.

Ten-Year Follow-Up of Taliglucerase Alfa in Type 1 Gaucher Disease: Real-World Evidence from Albania.

Journal: Journal of clinical medicine
Published: September 02, 2025

Real-world experience of switching to taliglucerase among patients with Gaucher disease in Québec: A case series.

Real-world experience of switching to taliglucerase among patients with Gaucher disease in Québec: A case series.

Journal: Molecular genetics and metabolism reports
Published: January 03, 2025

Plant molecular farming: a promising frontier for orphan drug production.

Plant molecular farming: a promising frontier for orphan drug production.

Journal: Biotechnology letters
Published: August 01, 2024

Taliglucerase alfa in the longterm treatment of children and adolescents with type 1 Gaucher disease: the Albanian experience.

Taliglucerase alfa in the longterm treatment of children and adolescents with type 1 Gaucher disease: the Albanian experience.

Journal: Frontiers in pediatrics
Published: December 07, 2023

Skeletal Manifestations, Bone Pain, and BMD Changes in Albanian Type 1 Gaucher Patients Treated with Taliglucerase Alfa.

Skeletal Manifestations, Bone Pain, and BMD Changes in Albanian Type 1 Gaucher Patients Treated with Taliglucerase Alfa.

Journal: Journal of osteoporosis
Published: October 03, 2023

Real-World Experiences with Taliglucerase Alfa Home Infusions for Patients with Gaucher Disease: A Global Cohort Study.

Real-World Experiences with Taliglucerase Alfa Home Infusions for Patients with Gaucher Disease: A Global Cohort Study.

Journal: Journal of clinical medicine
Published: August 02, 2023

The Bone Biomarker of Quantitative Chemical Shift Imaging in Patients with Type 1 Gaucher Disease Receiving Low-Dose Long-Term Enzyme Replacement Therapy.

The Bone Biomarker of Quantitative Chemical Shift Imaging in Patients with Type 1 Gaucher Disease Receiving Low-Dose Long-Term Enzyme Replacement Therapy.

Journal: Journal of clinical medicine
Published: January 05, 2023

A Systematic Review and Meta-analyses of Longitudinal Studies on Drug Treatments for Gaucher Disease.

A Systematic Review and Meta-analyses of Longitudinal Studies on Drug Treatments for Gaucher Disease.

Journal: The Annals of pharmacotherapy
Published: July 11, 2022

The budget impact of enzyme replacement therapy in type 1 Gaucher disease in the United States.

The budget impact of enzyme replacement therapy in type 1 Gaucher disease in the United States.

Journal: Journal of medical economics
Published: May 25, 2022

Safety and effectiveness of taliglucerase alfa in patients with Gaucher disease: an interim analysis of real-world data from a multinational drug registry (TALIAS).

Safety and effectiveness of taliglucerase alfa in patients with Gaucher disease: an interim analysis of real-world data from a multinational drug registry (TALIAS).

Journal: Orphanet journal of rare diseases
Published: December 20, 2021

Plant-Based COVID-19 Vaccines: Current Status, Design, and Development Strategies of Candidate Vaccines.

Plant-Based COVID-19 Vaccines: Current Status, Design, and Development Strategies of Candidate Vaccines.

Journal: Vaccines
Published: July 23, 2021

Impact of Long-Term Enzyme Replacement Therapy on Glucosylsphingosine (Lyso-Gb1) Values in Patients with Type 1 Gaucher Disease: Statistical Models for Comparing Three Enzymatic Formulations.

Impact of Long-Term Enzyme Replacement Therapy on Glucosylsphingosine (Lyso-Gb1) Values in Patients with Type 1 Gaucher Disease: Statistical Models for Comparing Three Enzymatic Formulations.

Journal: International journal of molecular sciences
Published: May 22, 2021
Showing 1-12 of 59

Last Updated: 10/31/2025