Voretigene Neparvovec-Rzyl

Last Updated: 09/26/2026

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Found 177 publications

Microperimetry is a valuable tool for assessing changes in visual function following voretigene neparvovec-rzyl gene therapy.

Microperimetry is a valuable tool for assessing changes in visual function following voretigene neparvovec-rzyl gene therapy.

Journal: Ophthalmic genetics

Published: June 16, 2026

Trends in the Engineering of Adeno-Associated Virus (AAV) for Precision Gene Delivery to the Central Nervous System (CNS).

Trends in the Engineering of Adeno-Associated Virus (AAV) for Precision Gene Delivery to the Central Nervous System (CNS).

Journal: International journal of molecular sciences

Published: May 07, 2026

Clinical experience with gene therapy for autosomal recessive RPE65-related retinal dystrophy in the Arabian Gulf.

Clinical experience with gene therapy for autosomal recessive RPE65-related retinal dystrophy in the Arabian Gulf.

Journal: Ophthalmology. Retina

Published: May 02, 2026

Interim Results From a Multicenter Observational Safety Study of Patients Treated With Voretigene Neparvovec-rzyl in the United States.

Interim Results From a Multicenter Observational Safety Study of Patients Treated With Voretigene Neparvovec-rzyl in the United States.

Journal: Ophthalmology

Published: April 27, 2026

Voretigene Neparvovec (Luxturna) for Biallelic RPE65-Associated Retinal Dystrophy: Systematic Review.

Voretigene Neparvovec (Luxturna) for Biallelic RPE65-Associated Retinal Dystrophy: Systematic Review.

Journal: American journal of ophthalmology

Published: April 26, 2026

Clinical and genetic characteristics of RPE65-associated inherited retinal degeneration in Koreans.

Clinical and genetic characteristics of RPE65-associated inherited retinal degeneration in Koreans.

Journal: Scientific reports

Published: April 23, 2026

Adeno-Associated Virus Gene Delivery to Hard-to-Transduce Tissues: Biological Barriers, Engineering Strategies, and Clinical Challenges.

Adeno-Associated Virus Gene Delivery to Hard-to-Transduce Tissues: Biological Barriers, Engineering Strategies, and Clinical Challenges.

Journal: Human gene therapy

Published: April 04, 2026

Precision Medicine in Inherited Retinal Disease: Advances, Challenges, and Future Directions.

Precision Medicine in Inherited Retinal Disease: Advances, Challenges, and Future Directions.

Journal: Journal of personalized medicine

Published: March 21, 2026

A heterozygous pathogenic RPE65 variant phenocopies a mitochondrial retinopathy.

A heterozygous pathogenic RPE65 variant phenocopies a mitochondrial retinopathy.

Journal: Ophthalmic genetics

Published: March 18, 2026

Four-Year Structural and Functional Outcomes of the First Subretinal Voretigene Neparvovec-rzyl Treatment for RPE65-Associated Inherited Retinal Dystrophy in Korea.

Four-Year Structural and Functional Outcomes of the First Subretinal Voretigene Neparvovec-rzyl Treatment for RPE65-Associated Inherited Retinal Dystrophy in Korea.

Journal: Korean journal of ophthalmology : KJO

Published: January 19, 2026

Vision Outcomes in Children Treated With Voretigene Neparvovec for RPE65-Associated Retinopathy.

Vision Outcomes in Children Treated With Voretigene Neparvovec for RPE65-Associated Retinopathy.

Journal: JAMA ophthalmology

Published: January 02, 2026

Gene-Agnostic Therapeutic Strategies for Inherited Retinal Diseases: Neuroprotection and Immunomodulation.

Gene-Agnostic Therapeutic Strategies for Inherited Retinal Diseases: Neuroprotection and Immunomodulation.

Journal: Genes

Published: January 01, 2026

Showing 1-12 of 177

Last Updated: 09/26/2026