Migalastat

Last Updated: 02/24/2026

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Found 147 publications

Navigating Fabry Disease in a Military Aviator.

Navigating Fabry Disease in a Military Aviator.

Journal: Aerospace medicine and human performance
Published: July 11, 2025

Long-Term Cardiac Stability Despite Late Enzyme Replacement Therapy in Fabry Disease With Severe Renal Involvement.

Long-Term Cardiac Stability Despite Late Enzyme Replacement Therapy in Fabry Disease With Severe Renal Involvement.

Journal: JACC. Case reports
Published: July 03, 2025

A Kidney Transplant Recipient Treated With Migalastat for Fabry Disease for 33 Months.

A Kidney Transplant Recipient Treated With Migalastat for Fabry Disease for 33 Months.

Journal: Experimental and clinical transplantation : official journal of the Middle East Society for Organ Transplantation
Published: June 23, 2025

Clinical Efficacy and Real-World Effectiveness of Fabry Disease Treatments: A Systematic Literature Review.

Clinical Efficacy and Real-World Effectiveness of Fabry Disease Treatments: A Systematic Literature Review.

Journal: Journal of clinical medicine
Published: May 23, 2025

Real-World Migalastat Use in Fabry Disease: Comparative Insights From the Pisani and Hughes Studies.

Real-World Migalastat Use in Fabry Disease: Comparative Insights From the Pisani and Hughes Studies.

Journal: Journal of inherited metabolic disease
Published: May 14, 2025

How to escape from sudden death: a challenging case of a rare cardiomyopathy with an unexpected twist.

How to escape from sudden death: a challenging case of a rare cardiomyopathy with an unexpected twist.

Journal: Monaldi archives for chest disease = Archivio Monaldi per le malattie del torace
Published: May 01, 2025

Hypertrophic Cardiomyopathy and Phenocopies: New Therapies for Old Diseases-Current Evidence and Future Perspectives.

Hypertrophic Cardiomyopathy and Phenocopies: New Therapies for Old Diseases-Current Evidence and Future Perspectives.

Journal: Journal of clinical medicine
Published: April 30, 2025

Clinical outcomes in Fabry patients switching to agalsidase beta for renal ineffectiveness of the primary Fabry therapy: a single-centre analysis.

Clinical outcomes in Fabry patients switching to agalsidase beta for renal ineffectiveness of the primary Fabry therapy: a single-centre analysis.

Journal: Clinical kidney journal
Published: April 24, 2025

Progress and Challenges in the Treatment of Fabry Disease.

Progress and Challenges in the Treatment of Fabry Disease.

Journal: BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapy
Published: April 09, 2025

Correction: Pharmacokinetic evaluation of single-dose migalastat in non-Fabry disease subjects with ESRD receiving dialysis treatment, and use of modeling to select dose regimens in Fabry disease subjects with ESRD receiving dialysis treatment.

Correction: Pharmacokinetic evaluation of single-dose migalastat in non-Fabry disease subjects with ESRD receiving dialysis treatment, and use of modeling to select dose regimens in Fabry disease subjects with ESRD receiving dialysis treatment.

Journal: PloS one
Published: April 08, 2025

Impact of migalastat on cerebral outcomes in fabry disease - results from the prospective observational FAMOUS trial.

Impact of migalastat on cerebral outcomes in fabry disease - results from the prospective observational FAMOUS trial.

Journal: Neurological research and practice
Published: March 27, 2025

Correction to "Clinical Outcomes in Patients Switching From Agalsidase Beta to Migalastat: A Fabry Registry Analysis".

Correction to "Clinical Outcomes in Patients Switching From Agalsidase Beta to Migalastat: A Fabry Registry Analysis".

Journal: Journal of inherited metabolic disease
Published: March 25, 2025
Showing 1-12 of 147

Last Updated: 02/24/2026