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Last Updated: 10/31/2025
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Found 364 publications
Reply to the Letter to the Editor: "Underlying Mechanism of Hypothyroidism in a Patient with ATTRv Receiving Patisiran".
Journal: Internal medicine (Tokyo, Japan)
Published: October 08, 2025
Underlying Mechanism of Hypothyroidism in a Patient with ATTRv Receiving Patisiran.
Journal: Internal medicine (Tokyo, Japan)
Published: October 08, 2025
Impact of patisiran on polyneuropathy of hereditary transthyretin amyloidosis in patients with a V122I or T60A variant: a phase IV multicenter study.
Journal: Annals of medicine
Published: September 20, 2025
Nanoparticle-Mediated siRNA Delivery in Human Epithelial Lung Cells Cultured at the Air-Liquid Interface.
Journal: Methods in molecular biology (Clifton, N.J.)
Published: August 28, 2025
Lipid nanoparticles for mRNA delivery in brain via systemic administration.
Journal: Science advances
Published: August 13, 2025
Standardizing a Protocol for Streamlined Synthesis and Characterization of Lipid Nanoparticles to Enable Preclinical Research and Education.
Journal: bioRxiv : the preprint server for biology
Published: August 06, 2025
Comparative Study on Cardiac Findings in Patients with Transthyretin Amyloidosis Before and After Treatment with a Transthyretin Silencer.
Journal: Journal of cardiovascular development and disease
Published: July 30, 2025
Temperature-controlled transition between non-denaturing and denaturing analysis of Patisiran on a mixed-mode SAX stationary phase utilizing two-dimensional liquid chromatography.
Journal: Journal of chromatography. A
Published: July 30, 2025
Development of Hypothyroidism in a Patient with ATTRv Amyloidosis Following Patisiran Administration.
Journal: Internal medicine (Tokyo, Japan)
Published: July 24, 2025
Realizing the therapeutic potential of rapid knockdown of transthyretin via RNA interference in transthyretin amyloidosis.
Journal: Molecular therapy. Nucleic acids
Published: July 21, 2025
Development of BMX siRNA lipid nanoparticles using novel ionizable and cleavable lipids discovered through AI and experimentation for cancer therapy.
Journal: International journal of pharmaceutics
Published: July 17, 2025
Real-world treatment management in hereditary transthyretin amyloidosis - an experience report and proposal for therapy switch decision criteria.
Journal: Neurological research and practice
Published: July 16, 2025
Last Updated: 10/31/2025