Velaglucerase

Last Updated: 04/28/2026

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Found 100 publications

Improvement of Bone Mineral Density in Patients with Type 1 Gaucher Disease Treated with Velaglucerase Alfa: Results from Clinical Studies.

Improvement of Bone Mineral Density in Patients with Type 1 Gaucher Disease Treated with Velaglucerase Alfa: Results from Clinical Studies.

Journal: Journal of clinical medicine

Published: January 19, 2026

Quantitative and Comparative Assessment of Recombinant Human β-Glucocerebrosidase Uptake Bioactivity Using a Stable hMMR-Expressing CHO Cell Model.

Quantitative and Comparative Assessment of Recombinant Human β-Glucocerebrosidase Uptake Bioactivity Using a Stable hMMR-Expressing CHO Cell Model.

Journal: Molecules (Basel, Switzerland)

Published: November 27, 2025

Bone involvement in Gaucher disease: Data from a North African registry.

Bone involvement in Gaucher disease: Data from a North African registry.

Journal: Reumatologia clinica

Published: July 17, 2025

Enzyme replacement therapy in infants and very young children with Gaucher disease using velaglucerase alfa: a single-center experience.

Enzyme replacement therapy in infants and very young children with Gaucher disease using velaglucerase alfa: a single-center experience.

Journal: Frontiers in pediatrics

Published: April 17, 2025

Assessing the Value for Money of Enzyme Replacement Therapy in Gaucher Disease Types 1 and 3b: Can Expanded Coverage Be Justified?

Assessing the Value for Money of Enzyme Replacement Therapy in Gaucher Disease Types 1 and 3b: Can Expanded Coverage Be Justified?

Journal: PharmacoEconomics - open

Published: April 08, 2025

Investigating the therapeutic profile of velaglucerase alfa in paediatric patients with Gaucher disease: a systematic review across all paediatric age groups.

Investigating the therapeutic profile of velaglucerase alfa in paediatric patients with Gaucher disease: a systematic review across all paediatric age groups.

Journal: Orphanet journal of rare diseases

Published: February 26, 2025

Effective encapsulation of therapeutic recombinant enzyme into polymeric nanoparticles as a potential vehicle for lysosomal disease treatment.

Effective encapsulation of therapeutic recombinant enzyme into polymeric nanoparticles as a potential vehicle for lysosomal disease treatment.

Journal: International journal of biological macromolecules

Published: August 14, 2024

Twelve Years of the Gaucher Outcomes Survey (GOS): Insights, Achievements, and Lessons Learned from a Global Patient Registry.

Twelve Years of the Gaucher Outcomes Survey (GOS): Insights, Achievements, and Lessons Learned from a Global Patient Registry.

Journal: Journal of clinical medicine

Published: April 19, 2024

A Real-World Investigation of MRI Changes in Bone in Patients with Type 1 Gaucher Disease Treated with Velaglucerase Alfa: The EIROS Study.

A Real-World Investigation of MRI Changes in Bone in Patients with Type 1 Gaucher Disease Treated with Velaglucerase Alfa: The EIROS Study.

Journal: Journal of clinical medicine

Published: April 08, 2024

Long-Term Treatment of Gaucher Disease with Velaglucerase Alfa in ERT-Naïve Patients from the Gaucher Outcome Survey (GOS) Registry.

Long-Term Treatment of Gaucher Disease with Velaglucerase Alfa in ERT-Naïve Patients from the Gaucher Outcome Survey (GOS) Registry.

Journal: Journal of clinical medicine

Published: March 25, 2024

Safety analysis of self-administered enzyme replacement therapy using data from the Fabry Outcome and Gaucher Outcome Surveys.

Safety analysis of self-administered enzyme replacement therapy using data from the Fabry Outcome and Gaucher Outcome Surveys.

Journal: Orphanet journal of rare diseases

Published: March 12, 2024

Evaluation of Lyso-Gb1 as a biomarker for Gaucher disease treatment outcomes using data from the Gaucher Outcome Survey.

Evaluation of Lyso-Gb1 as a biomarker for Gaucher disease treatment outcomes using data from the Gaucher Outcome Survey.

Journal: Orphanet journal of rare diseases

Published: February 19, 2024

Showing 1-12 of 100

Last Updated: 04/28/2026