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Last Updated: 10/31/2025
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Found 71 publications
Recent advances in mucopolysaccharidosis IVA treatment.
Journal: Orphanet journal of rare diseases
Published: June 05, 2025
Exploring Multivalent Architectures for Binding and Stabilization of N-Acetylgalactosamine 6-Sulfatase.
Journal: Molecules (Basel, Switzerland)
Published: March 31, 2025
Real-world treatment with elosulfase alfa in patients with MPS IVA is associated with improved endurance over time.
Journal: Genetics in medicine open
Published: November 08, 2024
Efficacy of different treatment strategies in patients with mucopolysaccharidosis: a systematic review and network meta-analysis of randomized controlled trials.
Journal: Orphanet journal of rare diseases
Published: October 15, 2024
Long-term outcomes of enzyme replacement therapy from a large cohort of Korean patients with mucopolysaccharidosis IVA (Morquio A syndrome).
Journal: Molecular genetics and metabolism reports
Published: September 25, 2024
Potential Targeting Mechanisms for Bone-Directed Therapies.
Journal: International journal of molecular sciences
Published: May 21, 2024
Bone Growth Induction in Mucopolysaccharidosis IVA Mouse.
Journal: International journal of molecular sciences
Published: April 17, 2023
Efficacy of Intravenous Elosulfase Alfa for Mucopolysaccharidosis Type IVA: A Systematic Review and Meta-Analysis.
Journal: Journal of personalized medicine
Published: July 25, 2022
Findings from the Morquio A Registry Study (MARS) after 6 years: Long-term outcomes of MPS IVA patients treated with elosulfase alfa.
Journal: Molecular genetics and metabolism
Published: May 17, 2022
Clinical characteristics and effects of enzyme replacement therapy with elosulfase alfa in Korean patients with mucopolysaccharidosis type IVA.
Journal: Molecular genetics and metabolism reports
Published: March 10, 2022
Consensus statement on enzyme replacement therapy for mucopolysaccharidosis IVA in Central and South-Eastern European countries.
Journal: Orphanet journal of rare diseases
Published: January 21, 2022
Successful Elosulfase Alfa Desensitization Protocol in a Patient With Morquio A Syndrome.
Journal: Pediatrics
Published: October 06, 2021
Last Updated: 10/31/2025