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Last Updated: 10/31/2025

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Found 72 publications

Thanatophoric Dysplasia Type 1 Treated with Vosoritide: A Case Report.

Thanatophoric Dysplasia Type 1 Treated with Vosoritide: A Case Report.

Journal: Hormone research in paediatrics
Published: September 02, 2025

Genetics of short stature.

Genetics of short stature.

Journal: Current opinion in pediatrics
Published: July 14, 2025

Vosoritide (Voxzogo) for Achondroplasia: A Review of Clinical and Real-World Evidence.

Vosoritide (Voxzogo) for Achondroplasia: A Review of Clinical and Real-World Evidence.

Journal: Cureus
Published: June 06, 2025

Changes in the Alignment of the Spine and Lower Limb in Children With Achondroplasia Treated With Vosoritide: A Single-center, 1-year Follow-up Prospective Study.

Changes in the Alignment of the Spine and Lower Limb in Children With Achondroplasia Treated With Vosoritide: A Single-center, 1-year Follow-up Prospective Study.

Journal: Journal of pediatric orthopedics
Published: April 15, 2025

Real-World Safety and Effectiveness of Vosoritide in Achondroplasia: Results from a Single Center in Portugal.

Real-World Safety and Effectiveness of Vosoritide in Achondroplasia: Results from a Single Center in Portugal.

Journal: Advances in therapy
Published: March 03, 2025

Sleep-disordered breathing in children with achondroplasia assessed by polysomnography: a retrospective chart review.

Sleep-disordered breathing in children with achondroplasia assessed by polysomnography: a retrospective chart review.

Journal: Archives of disease in childhood
Published: February 12, 2025

Real-World Evidence in New Drug and Biologics License Application Approvals During Fiscal Years 2020-2022.

Real-World Evidence in New Drug and Biologics License Application Approvals During Fiscal Years 2020-2022.

Journal: Clinical pharmacology and therapeutics
Published: February 12, 2025

Parental Perception of Quality of Life and Impact of Short Stature in Children with Hypochondroplasia and Other Genetic Causes of Short Stature.

Parental Perception of Quality of Life and Impact of Short Stature in Children with Hypochondroplasia and Other Genetic Causes of Short Stature.

Journal: Hormone research in paediatrics
Published: February 05, 2025

The CNP analogue vosoritide mediates PDE2-sensitive anti-arrhythmogenic effects in mouse hearts with STZ-induced type 1 diabetes.

The CNP analogue vosoritide mediates PDE2-sensitive anti-arrhythmogenic effects in mouse hearts with STZ-induced type 1 diabetes.

Journal: Basic research in cardiology
Published: January 30, 2025

International consensus guidelines on the implementation and monitoring of vosoritide therapy in individuals with achondroplasia.

International consensus guidelines on the implementation and monitoring of vosoritide therapy in individuals with achondroplasia.

Journal: Nature reviews. Endocrinology
Published: November 28, 2024

Functional Change in a Child With Achondroplasia Following 12 Months Treatment With Vosoritide-A Case Report.

Functional Change in a Child With Achondroplasia Following 12 Months Treatment With Vosoritide-A Case Report.

Journal: American journal of medical genetics. Part A
Published: November 21, 2024

Real-World Safety and Effectiveness of Vosoritide in Children with Achondroplasia: French Early Access Program.

Real-World Safety and Effectiveness of Vosoritide in Children with Achondroplasia: French Early Access Program.

Journal: Hormone research in paediatrics
Published: November 05, 2024
Showing 1-12 of 72

Last Updated: 10/31/2025