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Last Updated: 01/07/2026

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Found 76 publications

Effect of Vosoritide therapy on IGF-I and Endogenous C-type Natriuretic Peptide in Hypochondroplasia.

Effect of Vosoritide therapy on IGF-I and Endogenous C-type Natriuretic Peptide in Hypochondroplasia.

Journal: The Journal of clinical endocrinology and metabolism
Published: September 07, 2025

Thanatophoric Dysplasia Type 1 Treated with Vosoritide: A Case Report.

Thanatophoric Dysplasia Type 1 Treated with Vosoritide: A Case Report.

Journal: Hormone research in paediatrics
Published: September 02, 2025

Real-world safety and age-dependent effectiveness of vosoritide in achondroplasia: A single-center retrospective analysis of transition from growth hormone to vosoritide.

Real-world safety and age-dependent effectiveness of vosoritide in achondroplasia: A single-center retrospective analysis of transition from growth hormone to vosoritide.

Journal: Bone
Published: August 06, 2025

Genetics of short stature.

Genetics of short stature.

Journal: Current opinion in pediatrics
Published: July 14, 2025

C-type natriuretic peptide as mediator of growth in the absence of growth hormone: Unraveling the mystery of the growth without GH syndrome.

C-type natriuretic peptide as mediator of growth in the absence of growth hormone: Unraveling the mystery of the growth without GH syndrome.

Journal: Hormones (Athens, Greece)
Published: June 10, 2025

Vosoritide (Voxzogo) for Achondroplasia: A Review of Clinical and Real-World Evidence.

Vosoritide (Voxzogo) for Achondroplasia: A Review of Clinical and Real-World Evidence.

Journal: Cureus
Published: June 06, 2025

Changes in the Alignment of the Spine and Lower Limb in Children With Achondroplasia Treated With Vosoritide: A Single-center, 1-year Follow-up Prospective Study.

Changes in the Alignment of the Spine and Lower Limb in Children With Achondroplasia Treated With Vosoritide: A Single-center, 1-year Follow-up Prospective Study.

Journal: Journal of pediatric orthopedics
Published: April 15, 2025

Three-dimensional craniofacial imaging in children with achondroplasia treated with vosoritide.

Three-dimensional craniofacial imaging in children with achondroplasia treated with vosoritide.

Journal: Genetics in medicine open
Published: April 05, 2025

Real-World Safety and Effectiveness of Vosoritide in Achondroplasia: Results from a Single Center in Portugal.

Real-World Safety and Effectiveness of Vosoritide in Achondroplasia: Results from a Single Center in Portugal.

Journal: Advances in therapy
Published: March 03, 2025

Sleep-disordered breathing in children with achondroplasia assessed by polysomnography: a retrospective chart review.

Sleep-disordered breathing in children with achondroplasia assessed by polysomnography: a retrospective chart review.

Journal: Archives of disease in childhood
Published: February 12, 2025

Real-World Evidence in New Drug and Biologics License Application Approvals During Fiscal Years 2020-2022.

Real-World Evidence in New Drug and Biologics License Application Approvals During Fiscal Years 2020-2022.

Journal: Clinical pharmacology and therapeutics
Published: February 12, 2025

Parental Perception of Quality of Life and Impact of Short Stature in Children with Hypochondroplasia and Other Genetic Causes of Short Stature.

Parental Perception of Quality of Life and Impact of Short Stature in Children with Hypochondroplasia and Other Genetic Causes of Short Stature.

Journal: Hormone research in paediatrics
Published: February 05, 2025
Showing 1-12 of 76

Last Updated: 01/07/2026