Etranacogene Dezaparvovec

Last Updated: 02/24/2026

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Found 57 publications

CRISPR-Cas editing technologies for viral-mediated gene therapies of human diseases: Mechanisms, progress, and challenges.

CRISPR-Cas editing technologies for viral-mediated gene therapies of human diseases: Mechanisms, progress, and challenges.

Journal: Molecular therapy. Nucleic acids

Published: January 07, 2026

Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia B.

Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia B.

Journal: The New England journal of medicine

Published: December 08, 2025

Deconstructing gene therapy in hemophilia for the clinician.

Deconstructing gene therapy in hemophilia for the clinician.

Journal: Hematology. American Society of Hematology. Education Program

Published: December 05, 2025

Liver dysfunction in AAV-mediated Hemophilia B gene therapy: Mechanisms and management strategies.

Liver dysfunction in AAV-mediated Hemophilia B gene therapy: Mechanisms and management strategies.

Journal: Blood reviews

Published: September 08, 2025

Overview of gene therapy for hemophilia: questions and answers to navigate the innovation.

Overview of gene therapy for hemophilia: questions and answers to navigate the innovation.

Journal: Journal of thrombosis and haemostasis : JTH

Published: September 01, 2025

Long-term durability of rAAV gene therapy in hemophilia: Factor expression, clinical outcomes and underlying molecular mechanisms.

Long-term durability of rAAV gene therapy in hemophilia: Factor expression, clinical outcomes and underlying molecular mechanisms.

Journal: Blood reviews

Published: August 17, 2025

Curative Therapies for Hemophilias and Hemoglobinopathies in Adults: Immune, Gene, and Stem Cell Approaches in a Global Context.

Curative Therapies for Hemophilias and Hemoglobinopathies in Adults: Immune, Gene, and Stem Cell Approaches in a Global Context.

Journal: Biomedicines

Published: July 06, 2025

Fitusiran (Qfitlia) for hemophilia A and B.

Fitusiran (Qfitlia) for hemophilia A and B.

Journal: The Medical letter on drugs and therapeutics

Published: July 02, 2025

Advances in Gene Therapy Clinical Trials for Hemophilia Care.

Advances in Gene Therapy Clinical Trials for Hemophilia Care.

Journal: Current gene therapy

Published: May 08, 2025

Concizumab (Alhemo) for hemophilia A and B with inhibitors.

Concizumab (Alhemo) for hemophilia A and B with inhibitors.

Journal: The Medical letter on drugs and therapeutics

Published: May 05, 2025

Balancing Promise and Peril: Hemophilia Gene Therapy Insights.

Balancing Promise and Peril: Hemophilia Gene Therapy Insights.

Journal: IUBMB life

Published: April 09, 2025

Role of Pharmacy Professionals in Gene Therapy Based on Adeno-Associated Viruses: Treatment of Hemophilia as a Template of Care.

Role of Pharmacy Professionals in Gene Therapy Based on Adeno-Associated Viruses: Treatment of Hemophilia as a Template of Care.

Journal: The Canadian journal of hospital pharmacy

Published: March 19, 2025

Showing 1-12 of 57

Last Updated: 02/24/2026