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Last Updated: 10/31/2025
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Found 49 publications
Curative Therapies for Hemophilias and Hemoglobinopathies in Adults: Immune, Gene, and Stem Cell Approaches in a Global Context.
Journal: Biomedicines
Published: July 06, 2025
Fitusiran (Qfitlia) for hemophilia A and B.
Journal: The Medical letter on drugs and therapeutics
Published: July 02, 2025
Advances in Gene Therapy Clinical Trials for Hemophilia Care.
Journal: Current gene therapy
Published: May 08, 2025
Concizumab (Alhemo) for hemophilia A and B with inhibitors.
Journal: The Medical letter on drugs and therapeutics
Published: May 05, 2025
A Paradigm Shift in Hemophilia Care: The Promise of Gene Therapy.
Journal: Current gene therapy
Published: February 20, 2025
The deLIVERed promises of gene therapy: Past, present, and future of liver-directed gene therapy.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: February 11, 2025
Natural history of preexisting AAV5 antibodies in adults with hemophilia B during the lead-in of the etranacogene dezaparvovec phase 3 study.
Journal: Molecular therapy. Methods & clinical development
Published: February 10, 2025
Gene-ius at work: Hemophilia B treatment enters a new era.
Journal: American journal of health-system pharmacy : AJHP : official journal of the American Society of Health-System Pharmacists
Published: January 27, 2025
Marstacimab (Hympavzi) for hemophilia A and B.
Journal: The Medical letter on drugs and therapeutics
Published: January 03, 2025
Evaluation of One-Stage Assays for the Monitoring of Recombinant Human Factor IX Padua Activity After Etranacogene Dezaparvovec Gene Therapy.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: December 12, 2024
Evaluating the Cost-Effectiveness of Etranacogene Dezaparvovec Gene Therapy for Hemophilia B Treatment in the USA.
Journal: Applied health economics and health policy
Published: November 14, 2024
Last Updated: 10/31/2025