Trofinetide

Last Updated: 06/30/2026

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Found 76 publications

Rett syndrome and real-world treatment patterns of trofinetide in the United States.

Rett syndrome and real-world treatment patterns of trofinetide in the United States.

Journal: Journal of medical economics

Published: June 13, 2026

Real-World Treatment Landscape of Individuals with Rett Syndrome Treated and Untreated with Trofinetide in the United States.

Real-World Treatment Landscape of Individuals with Rett Syndrome Treated and Untreated with Trofinetide in the United States.

Journal: Journal of health economics and outcomes research

Published: April 23, 2026

Modulating alternative splicing of MECP2 is a potential therapeutic strategy for Rett syndrome.

Modulating alternative splicing of MECP2 is a potential therapeutic strategy for Rett syndrome.

Journal: Science translational medicine

Published: March 04, 2026

Drug-induced gastric motility disorders: A disproportionality analysis from the FAERS and CVARD databases.

Drug-induced gastric motility disorders: A disproportionality analysis from the FAERS and CVARD databases.

Journal: PloS one

Published: February 26, 2026

Hydrophobic Tag-Assisted Scalable Synthesis of Trofinetide and Its GPE Analogues.

Hydrophobic Tag-Assisted Scalable Synthesis of Trofinetide and Its GPE Analogues.

Journal: Journal of peptide science : an official publication of the European Peptide Society

Published: February 16, 2026

IGF1 peptide targets Rett Syndrome astrocytes to degrade IGF binding protein, rescue synaptogenesis and restore mitochondrial function.

IGF1 peptide targets Rett Syndrome astrocytes to degrade IGF binding protein, rescue synaptogenesis and restore mitochondrial function.

Journal: bioRxiv : the preprint server for biology

Published: February 09, 2026

Toward an NGF-based therapy for Rett syndrome.

Toward an NGF-based therapy for Rett syndrome.

Journal: Frontiers in neuroscience

Published: January 30, 2026

Insulin and Insulin-like Growth Factor 1 Signaling as a Modulator of MYC Expression in the Meibomian Gland.

Insulin and Insulin-like Growth Factor 1 Signaling as a Modulator of MYC Expression in the Meibomian Gland.

Journal: Biomedicines

Published: January 28, 2026

Clinical experience using trofinetide in Rett syndrome and related MECP2 diagnosis at the children's hospital of Philadelphia post approval.

Clinical experience using trofinetide in Rett syndrome and related MECP2 diagnosis at the children's hospital of Philadelphia post approval.

Journal: Frontiers in neurology

Published: December 26, 2025

Trofinetide-Induced Enterocolitis Syndrome in a Child with Rett Syndrome.

Trofinetide-Induced Enterocolitis Syndrome in a Child with Rett Syndrome.

Journal: Journal of child neurology

Published: December 22, 2025

Disease-modifying therapies for Rett syndrome: a review for neurologists.

Disease-modifying therapies for Rett syndrome: a review for neurologists.

Journal: Frontiers in neurology

Published: December 12, 2025

Design, synthesis and evaluation of trofinetide prodrug based on diketopiperazine strategy.

Design, synthesis and evaluation of trofinetide prodrug based on diketopiperazine strategy.

Journal: Bioorganic & medicinal chemistry

Published: November 18, 2025

Showing 1-12 of 76

Last Updated: 06/30/2026