Tofersen
Last Updated: 04/28/2026
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Found 122 publications
Fast and controlled access to tofersen for SOD1-related amyotrophic lateral sclerosis in The Netherlands; experiences using the orphan drug access protocol.
Journal: Amyotrophic lateral sclerosis & frontotemporal degeneration
Published: April 13, 2026
Longitudinal Analysis of Superoxide Dismutase 1 Seeding Activity in Amyotrophic Lateral Sclerosis Cerebrospinal Fluid.
Journal: medRxiv : the preprint server for health sciences
Published: April 03, 2026
Tofersen treatment in SOD1 p.Leu145Phe ALS: real-world outcomes in a genetically homogeneous Croatian cohort.
Journal: Amyotrophic lateral sclerosis & frontotemporal degeneration
Published: March 13, 2026
Long-Term Tofersen in SOD1 Amyotrophic Lateral Sclerosis.
Journal: JAMA neurology
Published: February 09, 2026
Tofersen: A Novel Option for the Treatment of Amyotrophic Lateral Sclerosis.
Journal: The Annals of pharmacotherapy
Published: February 05, 2026
Amyotrophic Lateral Sclerosis (ALS) Genetics and Microbiota: A Comprehensive Review.
Journal: International journal of molecular sciences
Published: February 03, 2026
Addendum to the 2023 clinical practice guidelines for amyotrophic lateral sclerosis in Japan: approval and integration of novel disease-modifying therapies.
Journal: Rinsho shinkeigaku = Clinical neurology
Published: January 21, 2026
Pharmacotherapy of neuromuscular diseases : what's new in 2025
Journal: Revue medicale suisse
Published: January 16, 2026
Tofersen, SOD1, and the Treatability of Amyotrophic Lateral Sclerosis.
Journal: JAMA neurology
Published: December 22, 2025
Facial-onset SOD1 amyotrophic lateral sclerosis: A case report and systematic review.
Journal: Journal of clinical neuroscience : official journal of the Neurosurgical Society of Australasia
Published: December 02, 2025
Amyotrophic lateral sclerosis in Saudi Arabia: a multicenter descriptive study.
Journal: Amyotrophic lateral sclerosis & frontotemporal degeneration
Published: November 24, 2025
Characterisation of Antisense Oligonucleotides by Ion-Pair Reversed-Phase UHPLC-HRMS: Method development using Design of Experiments.
Journal: Journal of mass spectrometry : JMS
Published: October 30, 2025
Last Updated: 04/28/2026