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Last Updated: 10/31/2025
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Found 62 publications
Dose-dependent effects of Arimoclomol in ALS: insights from a network meta-analysis.
Journal: Neurological sciences : official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology
Published: July 18, 2025
Game Changers: Blockbuster Small-Molecule Drugs Approved by the FDA in 2024.
Journal: Pharmaceuticals (Basel, Switzerland)
Published: April 20, 2025
Long-term efficacy and safety of arimoclomol in Niemann-Pick disease type C: Final results of the phase 2/3 NPC-002 48-month open-label extension trial.
Journal: Molecular genetics and metabolism
Published: March 17, 2025
Efficacy results from a 12-month double-blind randomized trial of arimoclomol for treatment of Niemann-Pick disease type C (NPC): Presenting a rescored 4-domain NPC Clinical Severity Scale.
Journal: Molecular genetics and metabolism reports
Published: February 10, 2025
Therapeutic Potential of Arimoclomol Nanomicelles: In Vitro Impact on Alzheimer's and Parkinson's Pathology and Correlation with In Vivo Inflammatory Response.
Journal: ACS chemical neuroscience
Published: February 05, 2025
Quantitative muscle magnetic resonance imaging as a biomarker for inclusion body myositis in clinical trials: exploring the in vivo effects of arimoclomol.
Journal: Clinical and experimental rheumatology
Published: January 25, 2025
Targeting lipid droplets in FUS-linked amyotrophic lateral sclerosis mitigates neuronal and astrocytic lipotoxicity.
Journal: Brain : a journal of neurology
Published: December 23, 2024
Arimoclomol Citrate.
Journal: American journal of health-system pharmacy : AJHP : official journal of the American Society of Health-System Pharmacists
Published: November 19, 2024
Safety and efficacy of arimoclomol in amyotrophic lateral sclerosis: a systematic review and meta-analysis.
Journal: Neurological sciences : official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology
Published: November 19, 2024
FDA approval of Miplyffa and Aqneursa: A dual breakthrough for the treatment of Neimann-Pick disease type C.
Journal: Alzheimer's & dementia (New York, N. Y.)
Published: November 09, 2024
Mechanistic insights into arimoclomol mediated effects on lysosomal function in Niemann-pick type C disease.
Journal: Molecular genetics and metabolism
Published: October 25, 2024
Last Updated: 10/31/2025