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Last Updated: 10/31/2025
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Found 7 publications
Levacetylleucine (N-acetyl-l-leucine) for Niemann-Pick disease type C.
Journal: Trends in pharmacological sciences
Published: February 07, 2025
2024 FDA TIDES (Peptides and Oligonucleotides) Harvest.
Journal: Pharmaceuticals (Basel, Switzerland)
Published: January 25, 2025
FDA approval of Miplyffa and Aqneursa: A dual breakthrough for the treatment of Neimann-Pick disease type C.
Journal: Alzheimer's & dementia (New York, N. Y.)
Published: November 09, 2024
Reply to "Levacetylleucine a game changer for Niemann-Pick disease type-C".
Journal: Brain & development
Published: October 29, 2024
Letter to the editor: "Levacetylleucine a game changer for Niemann pick disease type-C".
Journal: Brain & development
Published: October 11, 2024
Showing 1-7 of 7
Last Updated: 10/31/2025