Valoctocogene Roxaparvovec-Rvox
Last Updated: 04/28/2026
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Found 21 publications
Current Status of Clinical Gene Therapy for Hemophilia and Globin Disorders.
Journal: Journal of blood medicine
Published: October 22, 2025
Nonclinical toxicity study duration in AAV gene therapy development: Evidence from industry survey supports adequacy of short-term assessments.
Journal: Molecular therapy. Methods & clinical development
Published: August 14, 2025
Curative Therapies for Hemophilias and Hemoglobinopathies in Adults: Immune, Gene, and Stem Cell Approaches in a Global Context.
Journal: Biomedicines
Published: July 06, 2025
Fitusiran (Qfitlia) for hemophilia A and B.
Journal: The Medical letter on drugs and therapeutics
Published: July 02, 2025
Advances in Gene Therapy Clinical Trials for Hemophilia Care.
Journal: Current gene therapy
Published: May 08, 2025
Concizumab (Alhemo) for hemophilia A and B with inhibitors.
Journal: The Medical letter on drugs and therapeutics
Published: May 05, 2025
Balancing Promise and Peril: Hemophilia Gene Therapy Insights.
Journal: IUBMB life
Published: April 09, 2025
A Paradigm Shift in Hemophilia Care: The Promise of Gene Therapy.
Journal: Current gene therapy
Published: February 20, 2025
The deLIVERed promises of gene therapy: Past, present, and future of liver-directed gene therapy.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: February 11, 2025
Marstacimab (Hympavzi) for hemophilia A and B.
Journal: The Medical letter on drugs and therapeutics
Published: January 03, 2025
Marketing authorisation for rare diseases: The European regulatory perspective using the example of gene and cell therapies
Journal: Zeitschrift fur Evidenz, Fortbildung und Qualitat im Gesundheitswesen
Published: July 30, 2024
Last Updated: 04/28/2026