An Open-Label Study of Inhaled Treprostinil in Sarcoidosis Patients With Pulmonary Hypertension and Interstitial Lung Disease (SAPPHIRE)

Who is this study for? Patients with sarcoidosis-associated interstitial lung disease and pulmonary hypertension
What treatments are being studied? Inhaled Treprostinil
Status: Recruiting
Location: See location...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 2
SUMMARY

This study aims to evaluate the efficacy and safety of inhaled treprostinil in subjects with sarcoidosis-associated interstitial lung disease and pulmonary hypertension.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Maximum Age: 99
Healthy Volunteers: f
View:

• Study participant willing and able to provide informed consent

• Negative urine pregnancy test at baseline for females of childbearing potential

• Established diagnosis of sarcoidosis by ATS/ERS/WASOG 1999 Statement on of Sarcoidosis

• Presence of interstitial lung disease by Scadding Stage IV chest radiograph or extensive fibrosis on chest computed tomography

• Right heart catheterization within six months of baseline visit showing precapillary pulmonary hypertension (mPAP ≥ 25 mmHg, PCWP ≤ 15 mmHg, and PVR \> 3 WU)

• Patient on stable sarcoidosis therapy for at least three months prior to screening

• If patients are on oral PAH therapy (PDE5i/SCGS and/or ERA) then dose should be stable for at least three months prior to screening

• A 6MWT within three months of screening visit of \> 100 meters

Locations
United States
Florida
University of Florida, Division of Pulmonary and Critical Care Medicine
RECRUITING
Gainesville
Contact Information
Primary
Duncan R Lewis, BS
duncanlewis@ufl.edu
352-294-5195
Backup
Ali Ataya, MD
ali.ataya@medicine.ufl.edu
352-273-8740
Time Frame
Start Date: 2020-01-30
Estimated Completion Date: 2026-07-29
Participants
Target number of participants: 10
Treatments
Experimental: Study Group
Sarcoidosis patients with interstitial lung disease and precapillary pulmonary hypertension based on right heart catheterization (RHC).~All subjects will initiate inhaled treprostinil at a dose of 3 breaths (18 mcg) four times daily. Study drug doses escalations (additional one breath four times daily) can occur every three days with a maximum dosing regimen of up to 12 breaths (72 mcg) four times daily, as clinically tolerated.
Sponsors
Leads: University of Florida
Collaborators: United Therapeutics

This content was sourced from clinicaltrials.gov