Target ALS Biomarker Study; Longitudinal Biofluids, Clinical Measures, and At - Home Measures

Status: Recruiting
Location: See all (12) locations...
Study Type: Observational
SUMMARY

The goal of the study is to generate a biorepository of longitudinal biofluids-blood (plasma and serum), cerebral spinal fluid (CSF) and urine linked to genetics and longitudinal clinical information that are made available to the research community. To accomplish these goals, we will enroll 800 Amyotrophic Lateral Sclerosis (ALS) patients and 200 healthy controls from sites globally, over a 5 year time frame. Additionally, speech and motor function and spirometry measures will be collected bi-weekly in a subset of participants. ALS participants will be asked to come to the clinic for 5 study visits approximately every 4 months. Healthy participants will be coming for 2 study visits with a 12-month interval between visits. These samples and clinical information will be stored in a de-identified manner and made available for investigators to use in future research studies.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Healthy Volunteers: t
View:

⁃ ALS Participants:

• Age 18 or older.

• A diagnosis of ALS in accordance with Gold Coast criteria.

• Full Vital Capacity (FVC) of ≥30% or at the discretion of the Principal Investigator for the participant's predicted value for gender, height, and age at the time of screening.

• Ability to provide informed consent and understand the purpose and risks of the study.

• Ability to comply with study procedures and assessments, in the opinion of the Principal Investigator.

⁃ Healthy Control Participants:

• Age 18 or older.

• No history of neurological disease, in the opinion of the Principal Investigator.

• No known ALS- associated genetic mutations at the time of consent.

• Ability to provide informed consent and understand the purpose and risks of the study.

• Ability to comply with study procedures and assessments, in the opinion of the Principal Investigator.

Locations
United States
Arizona
Barrow Neurological Institute
RECRUITING
Phoenix
California
University of California San Diego
RECRUITING
San Diego
Washington, D.c.
Georgetown University
RECRUITING
Georgetown
Florida
Mayo Clinic
RECRUITING
Jacksonville
Illinois
Northwestern University
RECRUITING
Chicago
Massachusetts
Massachusetts General Hospital
RECRUITING
Boston
Missouri
Washington University
RECRUITING
St Louis
New York
Columbia University
RECRUITING
New York
Texas
Baylor College of Medicine
RECRUITING
Houston
Washington
University of Washington
RECRUITING
Seattle
Other Locations
Colombia
Instituto Roosevelt
RECRUITING
Bogotá
Puerto Rico
CHALS-CCT UPR MScience
RECRUITING
San Juan
Contact Information
Primary
Laura Dugom, MPH
laura.dugom@targetals.org
919-440-2073
Backup
Robert Bowser, PhD
robert.bowser@dignityhealth.org
602-406-8989
Time Frame
Start Date: 2021-06-01
Estimated Completion Date: 2031-12-31
Participants
Target number of participants: 1000
Treatments
Amyotrophic Lateral Sclerosis ALS
This is a global, multi-center study of ALS participants and healthy controls that will have up to 20 sites globally. Target enrollment will be approximately 1000 participants with 800 ALS participants and 200 healthy control cases. Research participants with suspected, possible, probable, probable- laboratory supported, and definite Amyotrophic Lateral Sclerosis (ALS), according to the revised El Escorial Criteria (EEC) or with a diagnosis based on the Gold Coast Criteria will be seen at the Screening/Baseline Visit(s) (Visit 1) and follow-up will occur at approximate 4-month internals for up to 5 visits per participant.
Healthy
Healthy control participants will have a neurological exam to confirm non-neurologic disease status and participants will have one follow up visit approximately 12 months after their baseline visit. Upon consenting for participation, all study participants will undergo the activities and biofluid collections at each visit.
Sponsors
Leads: Target ALS Foundation, Inc.

This content was sourced from clinicaltrials.gov