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  • Condition: Niemann-Pick Disease (NPD)
  • Journal: Orphanet journal of rare diseases
  • Treatment Used: Enzyme Replacement Therapy (ERT) with Olipudase Alfa
  • Number of Patients: 5
  • Published —
This study assessed the effect of enzyme replacement therapy (ERT) in patients with Niemann-Pick disease (enzyme disorder; NPD).

There are no recent clinical trials available for this condition. Please check back because new trials are being conducted frequently.