Treatment of Social and Language Deficits With Leucovorin for Young Children With Autism

Who is this study for? Infant patients with Autism Spectrum Disorder
What treatments are being studied? Levoleucovorin
Status: Recruiting
Location: See all (2) locations...
Intervention Type: Other, Drug
Study Type: Interventional
Study Phase: Phase 2
SUMMARY

The primary objective of this study is to evaluate the cognitive and behavioral effects of liquid leucovorin calcium on young children with autism spectrum disorder (ASD) and determine whether it improves social communication as well as the core and associated symptoms of ASD. The investigators will enroll 80 children across two sites, between the ages of 2.5 and 5 years, with confirmed ASD and known social and communication delays. Participation will last approximately 26 weeks, from screening visit to end of treatment.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 2
Maximum Age: 5
Healthy Volunteers: f
View:

• 1\. Autism Spectrum Disorder (diagnosed as Autistic Disorder on the ADOS-2 or the ADI-R).

• Between 2 years 6 months and 5 years 2 months of age at baseline

• Folate Receptor Alpha Autoantibody Positive status

• Language impairment (Ages and Stage Questionnaire between -1 and -3 SD for Language)

• English included in the languages in which the child is being raised

• Autism severity of moderate or higher (≥4) under the 7-item clinical global impression-severity scale. Moderate level of autism severity (4) is defined by the diagnosis of ASD with language impairment, so fulfilling #1 and #4 fulfills this requirement.

• Ability to maintain all ongoing complementary, dietary, traditional, and behavioral treatments constant for the study period

• Unchanged complementary, dietary, traditional, and behavioral treatments for two months prior to study entry

• Has at least 4 month old expressive language ability as assessed by the MSEL Expressive Language Scale (i.e., Parent answers yes to Voluntary babbling (such as 'bu, bu, bu) Question #7 on the MSEL Expressive Language Scale.

⁃ Ability to attend to social stimulus and tolerate imaging procedures, as determined at the discretion of the investigator

Locations
United States
Arizona
Southwestern Research & Resource Center
NOT_YET_RECRUITING
Phoenix
New York
State University of New York, Downstate
RECRUITING
Brooklyn
Contact Information
Primary
Richard E Frye, MD, PhD
DrFrye@RossignolMedicalCenter.com
(321) 259-7111
Time Frame
Start Date: 2020-10-08
Estimated Completion Date: 2026-06
Participants
Target number of participants: 80
Treatments
Experimental: L-leucovorin calcium
The liquid form of leucovorin calcium will be dosed by weight, with a target dose of 1mg/kg/day, divided into two daily doses. This product may be taken alone or mixed with liquid. Participants randomized to this arm will receive active treatment for both 12-week phases of the study.
Placebo_comparator: Placebo
The placebo will mimic the experimental treatment in flavor, odor, packaging, and dosing instructions. Participants randomized to this arm will receive placebo for the first 12 weeks of the study, then active treatment for the remaining 12 weeks.
Related Therapeutic Areas
Sponsors
Collaborators: State University of New York - Downstate Medical Center, Autism Speaks
Leads: Southwest Autism Research & Resource Center

This content was sourced from clinicaltrials.gov