A Prospective Prevalence Study in Adolescent and Adult Patients Dependent on Parenteral Nutrition to Assess the Incidence of Intestinal Failure-Associated Liver Disease

Status: Completed
Location: See all (15) locations...
Study Type: Observational
SUMMARY

This is a multi-center prospective cross-sectional observational study that will assess the prevalence of liver disease in patients dependent on parenteral nutrition (PN) for 4 or more days per week. Liver disease will be determined by the presence of choline deficiency, cholestasis (confirmed by elevated serum alkaline phosphatase (ALP) liver isoenzyme level), and steatosis (confirmed by magnetic resonance imaging-derived proton density fat fraction (MRI-PDFF). The objective of this study is to investigate the presence/prevalence of liver disease in patients dependent on PN (≥4 days a week).

Eligibility
Participation Requirements
Sex: All
Minimum Age: 12
Maximum Age: 80
Healthy Volunteers: f
View:

• The participant and/or their parent/Legally Authorized Representative is willing and able to provide signed informed consent or assent as appropriate

• Male or female adults 18 to 80 years of age, or adolescents 12 to 17 years of age

• Patients dependent on parenteral nutrition (PN) that receive PN for an average ≥ 4 days a week for 10 weeks or longer prior to screening to meet nutritional, caloric, fluid, and/or electrolyte needs

• The Investigator expects no changes in the lipid, dextrose, amino acid, or vitamin regimen to be medically necessary during the participant's participation in the study

• Willingness of participant to maintain his/her current habitual oral diet and fluids regimen for the study duration

Locations
United States
California
Ronald Reagan Medical Center of UCLA
Los Angeles
Florida
IHS Health
Kissimmee
Illinois
The University of Chicago
Chicago
Minnesota
Mayo Clinic
Rochester
North Carolina
Duke University Medical Center
Durham
Ohio
Cincinnati Children's Hospital
Cincinnati
Cleveland Clinic Foundation
Cleveland
Pennsylvania
UPMC Children's Hospital of Pittsburgh
Pittsburgh
Virginia
Virginia Commonwealth University
Richmond
Washington
Seattle Children's
Seattle
Other Locations
Denmark
Rigshospitalet
Copenhagen
Italy
Center for Chronic Intestinal Failure, St. Orsola Hospital Dept of Medical and Surgical Sciences, University of Bologna
Bologna
United Kingdom
St. Mark's Hospital
Harrow
University College London Hospitals
London
Northern Care Alliance NHS Foundation
Salford
Time Frame
Start Date: 2021-08-23
Completion Date: 2023-06-29
Participants
Target number of participants: 80
Related Therapeutic Areas
Sponsors
Leads: Protara Therapeutics

This content was sourced from clinicaltrials.gov