A Phase II Open-Label Randomized Study of Anti-Viral Antibiotic Therapy With and Without Familial (Maternal) Cytomegalovirus (CMV) Cytotoxic T Lymphocytes (CTLs) in Neonates With Moderate/Severe Maternal Acquired CMV Infection

Status: Recruiting
Location: See all (4) locations...
Intervention Type: Drug, Biological
Study Type: Interventional
Study Phase: Phase 2
SUMMARY

Patients with moderate or severe CMV disease less than 21 days old who have a maternal donor who has a CMV response to the peptivators will be screened. All patients will receive treatment with valganciclovir or ganciclovir. There is a safety run in with treatment with CMV CTLs in cohort 1 and if found to be safe, will proceed to cohort 2 for randomization to receive antiviral therapy with or without CMV CTLs. Funding source: FDA OOPD

Eligibility
Participation Requirements
Sex: All
Maximum Age: 21 days
Healthy Volunteers: f
View:

• Age: ≤ 21 days of life

• Birth Weight: ≥ 2500 gms

• Gestational age: ≥ 34 weeks of age

• Diagnosis of CMV viremia, viruria, and/or infection:Either one or more:

∙ Elevated CMV by RT-PCR in urine, saliva, CSF, or plasma; and/or Positive urine culture for CMV

∙ \- Moderate or Severe CMV Disease

∙ Any one or more of the following attributable to congenital CMV infection:

• Thrombocytopenia (≤ 50,000 mm3)

• Multiple petechiae

• Hepatomegaly

• Splenomegaly

• Intrauterine growth retardation

• Increased transaminases

• Increased bilirubin

• Microcephaly

• Ventriculomegaly

• Intracerebral calcifications

• Periventricular echogenicity

• Cortical or cerebral malformation

• Chorioretinitis

• Severe neonatal hearing loss

• CMV DNA by PCR in CNS

• Increased WBC for age in CNS

‣ Minimal Organ Criteria Hematological: ANC ≥ 750/mm3, HgB ≥ 8gm/dl, Platelets ≥ 20,000/kmm3 Renal: Serum creatinine ≤ 1.0 mg/dl Hepatic: ALT/SGOT ≤3x upper normal limits

⁃ Donor Availability: Maternal donor available with a T-cell response CMV MACS® PepTivators. the donor is considered suitable if the percentage of IFN-gamma+ T cells is \> 0.01% after stimulation with PepTivators.

Locations
United States
California
Children's Hospital Los Angeles
RECRUITING
Los Angeles
Missouri
Washington University
RECRUITING
St Louis
New York
New York Medical College
RECRUITING
Vallhala
Ohio
Nationwide Children's Hosptial
RECRUITING
Columbus
Contact Information
Primary
Mitchell Cairo, MD
mitchell_cairo@nymc.edu
914-594-2150
Backup
Edo Schaefer, MD
eshaefe@nymc.edu
Time Frame
Start Date: 2023-07-01
Estimated Completion Date: 2028-10-31
Participants
Target number of participants: 23
Treatments
Experimental: Cohort 1 Safety Run-in
The first 3 patients enrolled will receive both anti-viral medication and CMV CTLs, and treatment will be staggered every 28 days from the last dose of CMV CTLs from the prior patient.
Experimental: Cohort 2 Antiviral medication + CMV CTLs
Patients will receive both anti-viral medication and CMV CTLs
Active_comparator: Cohort 2 Antiviral medication only
Patients will only receive anti-viral therapy
Sponsors
Leads: New York Medical College

This content was sourced from clinicaltrials.gov