Condition 101 About Dystrophinopathy

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However, there may be experts who have treated this or similar conditions in our Find a Doctor section and research may be available in our Latest Advances section.

Top Global Doctors For Dystrophinopathy

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Latest Advances On Dystrophinopathy

  • Condition: Dystrophinopathies
  • Journal: Journal of neuromuscular diseases
  • Treatment Used: Physical Therapy
  • Number of Patients: 5
  • Published —
In this study, researchers sought to determine the best treatment for broken legs in boys with dystrophinopathies.
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Clinical Trials For Dystrophinopathy

Clinical Trial
  • Status: Recruiting
  • Participants: 2000
  • Start Date: July 1, 2019
A Registered Cohort Study on Duchenne Muscular Dystrophy
Clinical Trial
  • Status: Active, not recruiting
  • Phase: Phase 3
  • Intervention Type: Drug
  • Participants: 250
  • Start Date: July 6, 2017
A Phase 3, Randomized, Double-blind, Placebo-controlled Efficacy and Safety Study of Ataluren in Patients With Nonsense Mutation Duchenne Muscular Dystrophy and Open-Label Extension
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