A Placebo-Controlled, Double-Blind, Randomized, Phase 3 Study to Evaluate the Effect of 10 mg Obicetrapib in Participants With a History of HeFH Who Are Not Adequately Controlled by Their Lipid Modifying Therapies

Status: Completed
Location: See all (90) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 3
SUMMARY

This study will be a placebo-controlled, double-blind, randomized, phase 3 study to Evaluate the Efficacy, Safety, and Tolerability of Obicetrapib in Participants with a History of Heterozygous Familial Hypercholesterolemia (HeFH).

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Healthy Volunteers: f
View:

• Have a history of heterozygous familial hypercholesterolemia (HeFH) by 1) Genotyping (not a screening assessment), WHO Criteria/Dutch Lipid Clinical Network Criteria with a score of \> 8 points; and/or Simon Broome Register Diagnostic Criteria for definite or possible Familial Hypercholesterolemia (FH)

• Maximally tolerated lipid Modifying therapy for at least 8 weeks prior to screening such as: ATV (40 or 80), or (ROS 20 or 40 mg), Ezetimide, Bempedoic Acid, PCSK9 targeted therapy for at least 4 doses

• Fasting serum LDL-C ≥70 mg/dL (≥1.80 mmol/L)

Locations
United States
Arkansas
Site 01022
Jonesboro
California
Site 01015
Toluca Lake
Florida
Site 01009
Sarasota
Iowa
Site 01012
Iowa City
Idaho
Site 01023
Boise
Illinois
Site 01018
Chicago
Louisiana
Site 01007
Baton Rouge
Missouri
Site 01006
St Louis
Mississippi
Site 01005
Port Gibson
North Carolina
Site 01020
Morganton
Site 01019
Winston-salem
Nebraska
Site 01011
Lincoln
Site 01004
Norfolk
New Jersey
Site 01002
Morristown
Site 01010
New Providence
New York
Site 01001
North Massapequa
Tennessee
Site 01008
Chattanooga
Texas
Site 01016
El Paso
Site 01013
Houston
Virginia
Site 01014
Suffolk
Other Locations
Canada
Site 06007
Brampton
Site 06008
Chicoutimi
Site 06005
Halifax
Site 06003
Montreal
Site 06009
Montreal
Site 06004
Québec
Site 06006
Sherbrooke
Site 06001
Vancouver
Site 06002
Victoria
Georgia
Site 022001
Batumi
Site 022002
Tbilisi
Site 022003
Tbilisi
Site 022004
Tbilisi
Site 022005
Tbilisi
Site 022006
Tbilisi
Site 022007
Tbilisi
Site 022008
Tbilisi
Site 022009
Tbilisi
Site 022010
Tbilisi
Netherlands
Site 04001
Amsterdam
Site 04003
Arnhem
Site 04002
Deventer
Site 04004
Eindhoven
Site 04005
Roosendaal
Site 04006
Rotterdam
Norway
Site 023003
Bodø
Site 023002
Oslo
Poland
Site 05002
Bialystok
Site 05003
Lodz
Site 05004
Lodz
Site 05005
Zabrze
Site 05001
Zamość
South Africa
Site 018001
Bloemfontein
Site 018002
Cape Town
Site 018006
Centurion
Site 018009
Centurion
Site 018004
Parow
Site 018003
Somerset West
Site 018005
Somerset West
Site 018007
Tongaat
Site 018008
Umhlanga
Spain
Site 17004
A Coruña
Site 017001
Barcelona
Site 17002
Barcelona
Site 17003
Córdoba
Site 17018
Figueras
Site 17011
Granada
Site 17017
Huelva
Site 17012
Huesca
Site 17008
Las Palmas De Gran Canaria
Site 17010
Madrid
Site 17016
Madrid
Site 17007
Málaga
Site 17013
Sabadell
Site 17015
Santiago De Compostela
Site 17006
Seville
Site 17009
Seville
Site 17014
Valencia
Site 17005
Zaragoza
United Kingdom
Site 014006
Birmingham
Site 014012
Bristol
Site 014009
Cardiff
Site 014010
Chichester
Site 014001
Dundee
Site 014002
London
Site 014003
Manchester
Site 014008
Metropolitan Borough Of Wirral
Site 014011
Penzance
Site 014005
Stevenage
Site 014004
West Bromwich
Time Frame
Start Date: 2022-07-25
Completion Date: 2024-05-28
Participants
Target number of participants: 354
Treatments
Placebo_comparator: Placebo
one placebo tablet once daily
Experimental: Obicetrapib 10 mg
one 10 mg Obicetrapib tablet once daily
Sponsors
Leads: NewAmsterdam Pharma

This content was sourced from clinicaltrials.gov