MediFind
Condition

Latest Advances in Mucopolysaccharidosis Type 3

  • Overview
  • Find a Doctor
  • Latest Advances
  • Clinical Trials

Latest Advances

  • Condition: Sanfilippo Syndrome Type A
  • Journal: Molecular genetics and metabolism
  • Treatment Used: Intrathecal Heparan-N-Sulfatase (HNS)
  • Number of Patients: 21
  • Published — December 12, 2018
This study reported on the effectiveness , pharmacokinetics, safety, and tolerability of intrathecal (IT) administration of recombinant human heparan-N-sulfatase (rhHNS) in the treatment of Sanfilippo syndrome type A (mucopolysaccharidosis type IIIA), a lysosomal disorder associated with progressive neurodegeneration in early childhood.
Showing 1-1 of 1
ClickClickClickClickClick
Find better care, faster.
  • How MediFind Works
  • Our Story
  • Conditions A-Z
  • Doctor Directory
  • Newsroom
  • Partnering With Us
  • Contact Us
Subscribe to our newsletter

Sign up to stay informed about MediFind and get wellness sent your way.

By subscribing, I agree to MediFind's Terms & Conditions and Privacy Policy.

  • FAQ
  • Feedback
  • Advertising Policy
  • Privacy Policy
  • Terms & Conditions
Follow Us On
MediFindFind better care, faster.
© 2021 All Rights Reserved.

This information is not intended as a substitute for informed medical advice. You should work with a licensed professional to diagnose and treat health conditions.