Mucopolysaccharidosis Type 3 (MPS III, Sanfilippo Syndrome)Symptoms, Doctors, Treatments, Advances & More
Mucopolysaccharidosis Type 3 (MPS III, Sanfilippo Syndrome) Overview
Learn About Mucopolysaccharidosis Type 3 (MPS III, Sanfilippo Syndrome)
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However, there may be experts who have treated this or similar conditions in our Find a Doctor section and research may be available in our Latest Advances section.
Kristen Truxal is a Medical Genetics specialist and a Pediatrics provider practicing medicine in Lima, Ohio. Dr. Truxal is rated as an Elite provider by MediFind in the treatment of Mucopolysaccharidosis Type 3 (MPS III, Sanfilippo Syndrome). She is also highly rated in 4 other conditions, according to our data. Her clinical expertise encompasses Mucopolysaccharidosis Type 3 (MPS III, Sanfilippo Syndrome), Mucopolysaccharidosis Type 3A (MPS IIIA, Sanfilippo Syndrome A), Mucopolysaccharidoses (MPS), and Mucopolysaccharidosis Type 3B (MPS IIIB, Sanfilippo Syndrome B). Dr. Truxal is board certified in American Board Of Pediatrics. Dr. Truxal is currently accepting new patients.
Washington University Physicians In Illinois Inc
Patricia Dickson is a Medical Genetics specialist and a Pediatrics provider practicing medicine in Belleville, Illinois. Dr. Dickson is rated as an Elite provider by MediFind in the treatment of Mucopolysaccharidosis Type 3 (MPS III, Sanfilippo Syndrome). She is also highly rated in 12 other conditions, according to our data. Her clinical expertise encompasses Mucopolysaccharidosis Type 1 (MPS I, Hurler Syndrome), Mucopolysaccharidoses (MPS), Mucopolysaccharidosis Type 3 (MPS III, Sanfilippo Syndrome), and Mucopolysaccharidosis Type 3B (MPS IIIB, Sanfilippo Syndrome B). Dr. Dickson is currently accepting new patients.
Brian Bigger practices practicing medicine in Edinburgh, United Kingdom. Mr. Bigger is rated as an Elite expert by MediFind in the treatment of Mucopolysaccharidosis Type 3 (MPS III, Sanfilippo Syndrome). He is also highly rated in 13 other conditions, according to our data. His clinical expertise encompasses Mucopolysaccharidoses (MPS), Mucopolysaccharidosis Type 3 (MPS III, Sanfilippo Syndrome), Mucopolysaccharidosis Type 3A (MPS IIIA, Sanfilippo Syndrome A), Mucopolysaccharidosis Type 2 (MPS II, Hunter Syndrome), and Bone Marrow Transplant.
Summary: The goal of this clinical trial is to test cannabidiol in Sanfilippo syndrome. The main questions it aims to answer are: 1) determine the safety of cannabidiol in Sanfilippo syndrome, and 2) explore the efficacy of cannabidiol in treating the neurobehavioral symptoms and functional outcomes of Sanfilippo syndrome. Each participant's caregiver will be asked to complete surveys related to the partic...
Summary: The main objective of this study is to evaluate the efficacy and safety of UX111 for the treatment of MPS IIIA.