Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy (DeQoDE-DM)

Status: Recruiting
Location: See location...
Study Type: Observational
SUMMARY

Myotonic dystrophy (dystrophia myotonica; DM), the most prevalent form of muscular dystrophy in adults, is characterized by progressive myopathy, myotonia, and multi-systemic involvement. DM causes severe disability and profoundly affects the patient's quality of life. Currently, no effective treatments are available that alter the course of the disease, but ongoing clinical trials are underway.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Maximum Age: 65
Healthy Volunteers: t
View:

⁃ DM subjects

• Age 18 - 65 years

• Diagnosis of DM1 or DM2 by clinical or genetic criteria. If DM1 or DM2 was diagnosed by clinical criteria, a first-degree relative must have genetic testing confirmation and sign a genetic consent form to release their genetic information

• Clinically affected, as defined by muscle weakness or myotonia

• Ambulate independently (a walker is not permitted)

• Able to provide informed consent for participation in the study

⁃ Control subjects

• Age 18 - 65 years old

• Healthy as defined by no significant medical or neurological conditions

• Able to provide informed consent for participation in the study

Locations
United States
North Carolina
Wake Forest University Health Sciences
RECRUITING
Winston-salem
Contact Information
Primary
Elizabeth (Gracie) G Hilber
Elizabeth.Hilber@Advocatehealth.org
336-716-4163
Backup
Constance Linville
Martha.Linville@advocatehealth.org
704-355-2000
Time Frame
Start Date: 2025-05-15
Estimated Completion Date: 2029-05
Participants
Target number of participants: 75
Treatments
DM subjects
1. Age 18 - 65 years~2. Diagnosis of DM1 or DM2 by clinical or genetic criteria. If DM1 or DM2 was diagnosed by clinical criteria, a first-degree relative must have genetic testing confirmation and sign a genetic consent form to release their genetic information.~3. Clinically affected, as defined by muscle weakness or myotonia~4. Ambulate independently (a walker is not permitted)~5. Able to provide informed consent for participation in the study
Control subjects
1. Age 18 - 65 years old~2. Healthy as defined by no significant medical or neurological conditions~3. Able to provide informed consent for participation in the study
Sponsors
Leads: Wake Forest University Health Sciences

This content was sourced from clinicaltrials.gov